{"id":"W1943135484","doi":"10.1002/mus.23904","title":"SMA valiant trial: A prospective, double‐blind, placebo‐controlled trial of valproic acid in ambulatory adults with spinal muscular atrophy","year":2013,"lang":"en","type":"article","venue":"Muscle & Nerve","topic":"Neurogenetic and Muscular Disorders Research","field":"Medicine","cited_by":76,"is_retracted":false,"has_abstract":true,"ca_institutions":"Centre Hospitalier Universitaire Sainte-Justine; University of Manitoba","funders":"Eunice Kennedy Shriver National Institute of Child Health and Human Development; National Center for Research Resources; National Center for Advancing Translational Sciences; National Institute of Neurological Disorders and Stroke","keywords":"Spinal muscular atrophy; SMA*; Medicine; Placebo; Ambulatory; Valproic Acid; Isometric exercise; Physical therapy; Clinical trial; Internal medicine; Anesthesia; Epilepsy; Pathology","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.001074315,0.001092121,0.002166506,0.0002659817,0.0003715997,0.0006932221,0.0004809767,0.001174537,0.004064916],"category_scores_gemma":[0.0009801493,0.0004006126,0.0009980943,0.0002739002,0.0006158257,0.0004998363,0.0002389863,0.001584539,0.0006509068],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0002647021,"about_ca_system_score_gemma":0.0006541814,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.0004132856,"about_ca_topic_score_gemma":0.0009382117,"domain_scores_codex":[0.9996843,0.0001662743,0.00003200947,0.00005275074,0.00003128166,0.00003337386],"domain_scores_gemma":[0.9995509,0.0001007819,0.0001396019,0.00003330363,0.00003357822,0.000141737],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"randomized_trial","study_design_gemma":"randomized_trial","study_design_scores_codex":[0.9723293,0.003143066,0.001326254,0.001164249,0.001054817,0.00005710765,0.00004378394,0.0001586068,0.006082151,0.00009547583,0.0005881584,0.01395701],"study_design_scores_gemma":[0.9517418,0.04337264,0.003427381,0.00004625329,0.0003642245,0.00004821945,0.00001131505,0.0001304315,0.000326506,0.00004693761,0.0004783629,0.000005951563],"study_design_candidate":"randomized_trial","study_design_consensus":"randomized_trial","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9829785,0.01136896,0.0004701829,0.0004988922,0.0003479548,0.001529316,0.001019772,0.0000864428,0.001700037],"genre_scores_gemma":[0.9855202,0.004963137,0.001605393,0.0009572948,0.0005585199,0.00275256,0.001373525,0.0000162633,0.002253102],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.004064916,"threshold_uncertainty_score":0.0135985,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.0230891315939462,"score_gpt":0.2891402743874028,"score_spread":0.2660511427934566,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}