{"id":"W1969271703","doi":"10.1056/nejmoa1407309","title":"Long-Term Safety and Efficacy of Factor IX Gene Therapy in Hemophilia B","year":2014,"lang":"en","type":"article","venue":"New England Journal of Medicine","topic":"Hemophilia Treatment and Research","field":"Medicine","cited_by":1250,"is_retracted":false,"has_abstract":true,"ca_institutions":"St. Thomas Hospital","funders":"National Cancer Institute; National Heart, Lung, and Blood Institute; Medical Research Council; University College London Hospitals NHS Foundation Trust; National Institute for Health and Care Research; American Lebanese Syrian Associated Charities; Assisi Foundation of Memphis; NHS Blood and Transplant; University College London; Howard Hughes Medical Institute","keywords":"Factor IX; Medicine; Genetic enhancement; Internal medicine; Gastroenterology; Toxicity; Adverse effect; Surgery; Gene","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.03263389734612409,"score_gpt":0.3254365059104377,"score_spread":0.2928026085643136,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}