{"id":"W1994774399","doi":"10.1016/j.nmd.2007.10.006","title":"Adenovirus and adeno-associated virus-mediated delivery of human myophosphorylase cDNA and LacZ cDNA to muscle in the ovine model of McArdle’s disease: Expression and re-expression of glycogen phosphorylase","year":2008,"lang":"en","type":"article","venue":"Neuromuscular Disorders","topic":"Glycogen Storage Diseases and Myoclonus","field":"Medicine","cited_by":32,"is_retracted":false,"has_abstract":false,"ca_institutions":"Montreal Neurological Institute and Hospital; McGill University","funders":"Murdoch University","keywords":"Complementary DNA; Adeno-associated virus; Glycogen phosphorylase; Biology; Glycogen storage disease; Glycogenolysis; Glycogen; lac operon; Molecular biology; Gene expression; Gene; Vector (molecular biology); Genetics; Biochemistry; Recombinant DNA","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0005783993,0.0005215841,0.0004274224,0.0006002102,0.0003497644,0.0006112258,0.0005218703,0.001089451,0.001829239],"category_scores_gemma":[0.000372316,0.0003473793,0.0005256332,0.0003087216,0.0008414239,0.0006475414,0.0003051441,0.001432027,0.0003828432],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.000763996,"about_ca_system_score_gemma":0.000658196,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.001372371,"about_ca_topic_score_gemma":0.002058445,"domain_scores_codex":[0.9995801,0.00007038203,0.00006610613,0.0001140762,0.00006820769,0.0001011174],"domain_scores_gemma":[0.9996614,0.00009532014,0.00009542656,0.00005708759,0.00002060216,0.00007014016],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"bench_or_experimental","study_design_gemma":"bench_or_experimental","study_design_scores_codex":[0.0009979418,0.0001636318,0.0002023273,0.00009219046,0.00001789836,0.0002224726,0.0001171281,0.0001018715,0.9946811,0.001427705,0.000114202,0.001861628],"study_design_scores_gemma":[0.0003133624,0.00187184,0.001693487,0.00002118086,0.0000660071,0.0008045062,0.00009704904,0.001000126,0.9841449,0.0001728368,0.009796537,0.00001821761],"study_design_candidate":"bench_or_experimental","study_design_consensus":"bench_or_experimental","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9885613,0.00219903,0.005603345,0.000323528,0.000378539,0.0001999424,0.0007493683,0.0001074525,0.00187751],"genre_scores_gemma":[0.9753125,0.001496206,0.01103157,0.00008948449,0.00004872956,0.0002929345,0.001476544,0.00006190494,0.01019017],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.001829239,"threshold_uncertainty_score":0.00611943,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.01645883857121551,"score_gpt":0.2384912799814664,"score_spread":0.2220324414102509,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}