{"id":"W2016634375","doi":"10.1016/s0140-6736(15)60297-5","title":"Rare diseases and effective treatments: are we delivering?","year":2015,"lang":"en","type":"article","venue":"The Lancet","topic":"Complement system in diseases","field":"Immunology and Microbiology","cited_by":60,"is_retracted":false,"has_abstract":false,"ca_institutions":"Hospital for Sick Children","funders":"","keywords":"Medicine; European union; Medical prescription; Antibiotic resistance; European commission; Rare disease; Family medicine; Intensive care medicine; Pediatrics; Antibiotics; Disease; Pathology; Business; Biology; Pharmacology","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"codex-gemma-dda1882f352a","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.00006806473,0.0001003985,0.0002320357,0.00001806196,0.00009732188,0.00001440296,0.0001570894,0.00002834975,0.0001166031],"category_scores_gemma":[0.00006025275,0.0000611963,0.00003015733,0.00003716144,0.00009570999,0.00004100494,0.0001066824,0.00005093598,0.0002018714],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.00003488717,"about_ca_system_score_gemma":0.00001197994,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.00004630917,"about_ca_topic_score_gemma":0.00001401652,"domain_scores_codex":[0.9993778,0.0002024887,0.00007849067,0.0001407394,0.00002288922,0.0001776031],"domain_scores_gemma":[0.9994622,0.0001402887,0.00005439984,0.0002889478,0.00002813914,0.00002598204],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"observational","study_design_gemma":"observational","study_design_scores_codex":[0.0006956874,0.0001441404,0.7817012,0.00007161796,0.0005191076,0.000018814,0.001037229,0.00000941276,0.001496341,0.000573311,0.2086189,0.005114219],"study_design_scores_gemma":[0.005347217,0.0002210292,0.8781506,0.0001608117,0.0002538446,0.00004453181,0.001182436,0.000004863718,0.001039704,0.001417628,0.1119807,0.000196591],"study_design_candidate":"observational","study_design_consensus":"observational","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9747333,0.02206401,0.00001177275,0.00136678,0.0002949823,0.0004117225,0.0003479233,0.00009828839,0.0006712477],"genre_scores_gemma":[0.999008,0.0001232697,0.000006388546,0.0001819293,0.0001252049,0.00009450477,0.00003920233,0.00000734536,0.0004141369],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.09663823,"threshold_uncertainty_score":0.2594716,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.03824806269975924,"score_gpt":0.2844943919378012,"score_spread":0.246246329238042,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}