{"id":"W2019242604","doi":"10.1016/j.jacl.2012.02.006","title":"Cholesterol trapping in Niemann-Pick disease type B fibroblasts can be relieved by expressing the phosphotyrosine binding domain of GULP","year":2012,"lang":"en","type":"article","venue":"Journal of clinical lipidology","topic":"Lysosomal Storage Disorders Research","field":"Medicine","cited_by":6,"is_retracted":false,"has_abstract":false,"ca_institutions":"Royal Victoria Hospital; Royal Victoria Regional Health Centre; McGill University","funders":"Canadian Institutes of Health Research","keywords":"Medicine; Cancer research","routes":{"ca_aff":true,"ca_fund":true,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0002900596,0.0004682625,0.0003020652,0.0003034351,0.0004527669,0.0005519939,0.0004151622,0.0005235291,0.001461469],"category_scores_gemma":[0.0002291909,0.0002823841,0.0002865654,0.0002066734,0.0004131384,0.0003007172,0.0003633534,0.0008014697,0.0009038346],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0003710284,"about_ca_system_score_gemma":0.0003830901,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.001758258,"about_ca_topic_score_gemma":0.002114614,"domain_scores_codex":[0.9997568,0.000056237,0.00004935909,0.00002429376,0.00006397044,0.00004940269],"domain_scores_gemma":[0.999723,0.00006769703,0.00005856204,0.00005206073,0.00002102587,0.00007767663],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"bench_or_experimental","study_design_gemma":"bench_or_experimental","study_design_scores_codex":[0.0001924945,0.0000433032,0.0000881532,0.00002953931,0.000007048453,0.0002188922,0.00002885765,0.00005671886,0.9986516,0.0001260646,0.00007588526,0.0004815168],"study_design_scores_gemma":[0.0000893247,0.0001873129,0.001833896,0.000009036293,0.00002182967,0.0007658486,0.0000809851,0.001095803,0.9928504,0.00006980034,0.002985086,0.00001068316],"study_design_candidate":"bench_or_experimental","study_design_consensus":"bench_or_experimental","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9953962,0.0008391549,0.001298641,0.0002908065,0.00006431683,0.00002055425,0.0006343057,0.00009417131,0.001361828],"genre_scores_gemma":[0.9946901,0.0004855678,0.001525684,0.00007885622,0.00001663018,0.00003613718,0.0007942655,0.00003954415,0.002333307],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.001758258,"threshold_uncertainty_score":0.004889131,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.09243287201142239,"score_gpt":0.4098723468506847,"score_spread":0.3174394748392623,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}