{"id":"W2025763389","doi":"10.1089/hum.2006.17.487","title":"Correction of Feline Lipoprotein Lipase Deficiency with Adeno-Associated Virus Serotype 1-Mediated Gene Transfer of the Lipoprotein Lipase S447X Beneficial Mutation","year":2006,"lang":"en","type":"article","venue":"Human Gene Therapy","topic":"Virus-based gene therapy research","field":"Biochemistry, Genetics and Molecular Biology","cited_by":81,"is_retracted":false,"has_abstract":true,"ca_institutions":"University of British Columbia","funders":"Dainippon Sumitomo Pharma","keywords":"Lipoprotein lipase; Lipase; Serotype; Mutation; Virology; Gene; Genetic enhancement; Biology; Genetics; Medicine; Enzyme; Biochemistry","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.000327274,0.0005015986,0.0004510427,0.0004496904,0.0001891896,0.0003416938,0.0004605559,0.000841663,0.001571612],"category_scores_gemma":[0.0003350009,0.0001959606,0.0004001331,0.0001233626,0.0005860332,0.0002914412,0.0002571086,0.0007435023,0.0003751089],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0006285893,"about_ca_system_score_gemma":0.0004644255,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.001853762,"about_ca_topic_score_gemma":0.002087757,"domain_scores_codex":[0.9997403,0.00004544223,0.00002520005,0.00006128716,0.0000640267,0.00006385912],"domain_scores_gemma":[0.9997995,0.00004022121,0.00007130077,0.00001978703,0.00001700016,0.00005208578],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"bench_or_experimental","study_design_gemma":"bench_or_experimental","study_design_scores_codex":[0.0002534427,0.0001186323,0.0005027606,0.00009585212,0.00001733837,0.0004061587,0.00004351435,0.0002437964,0.9934477,0.0003248526,0.0001668095,0.004379158],"study_design_scores_gemma":[0.0002285746,0.004742976,0.005728202,0.00003959391,0.0000881236,0.003303263,0.0001088388,0.003971328,0.9734945,0.000211456,0.008056901,0.00002626018],"study_design_candidate":"bench_or_experimental","study_design_consensus":"bench_or_experimental","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9928482,0.001095242,0.003721815,0.0003240425,0.00008290145,0.0001382005,0.0002974092,0.0002864671,0.001205755],"genre_scores_gemma":[0.9886578,0.001078029,0.005715583,0.000133846,0.00003535453,0.0001410388,0.0005604445,0.00003752424,0.003640384],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.001853762,"threshold_uncertainty_score":0.005257607,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.01350715953197388,"score_gpt":0.2535930466997071,"score_spread":0.2400858871677332,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}