{"id":"W2034365623","doi":"10.1038/gim.2013.148","title":"“Is a cure in my sight?” Multi-stakeholder perspectives on phase I choroideremia gene transfer clinical trials","year":2013,"lang":"en","type":"article","venue":"Genetics in Medicine","topic":"Retinal Development and Disorders","field":"Biochemistry, Genetics and Molecular Biology","cited_by":27,"is_retracted":false,"has_abstract":true,"ca_institutions":"Royal Alexandra Hospital; University of Alberta","funders":"Canadian Institutes of Health Research; Alberta Innovates; University of Alberta; Ministry of Advanced Education, Government of Alberta","keywords":"Choroideremia; Medicine; Clinical trial; Gene transfer; Harm; Intensive care medicine; Ophthalmology; Psychology; Internal medicine; Genetics; Gene","routes":{"ca_aff":true,"ca_fund":true,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.1107046,0.0007234114,0.0008194951,0.001048624,0.01710682,0.01148616,0.001738023,0.01148972,0.00265433],"category_scores_gemma":[0.102672,0.0007531705,0.001090216,0.0007445272,0.02418385,0.01056901,0.01063794,0.01860373,0.0003911416],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.006785791,"about_ca_system_score_gemma":0.01205999,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.001879075,"about_ca_topic_score_gemma":0.002097826,"domain_scores_codex":[0.7913166,0.1925055,0.002625213,0.002227103,0.006402448,0.00492318],"domain_scores_gemma":[0.8162174,0.150167,0.01124355,0.001801165,0.008549104,0.01202177],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"qualitative","study_design_gemma":"qualitative","study_design_scores_codex":[0.0003098492,0.0001601642,0.006047712,0.0006123863,0.0001193192,0.004971011,0.8922377,0.0004406258,0.002687575,0.05371825,0.01664404,0.02205142],"study_design_scores_gemma":[0.00009568823,0.0004203967,0.002177197,0.001372425,0.00008868251,0.00350834,0.8209102,0.0006479661,0.001494499,0.03292161,0.1362141,0.0001489178],"study_design_candidate":"qualitative","study_design_consensus":"qualitative","genre_codex":"commentary","genre_gemma":"empirical","genre_scores_codex":[0.2590426,0.008545078,0.01154096,0.6815103,0.002285602,0.0002200974,0.00006227601,0.00004143882,0.03675159],"genre_scores_gemma":[0.9403941,0.002636722,0.002072679,0.05294752,0.0006509196,0.0001345963,0.00001680373,0.00002475372,0.001121925],"genre_candidate":"empirical","genre_consensus":null,"teacher_disagreement_score":0.1107046,"threshold_uncertainty_score":0.5854688,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.2043004282884719,"score_gpt":0.4479528612251884,"score_spread":0.2436524329367165,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}