{"id":"W2050265892","doi":"10.1016/j.clim.2006.04.317","title":"Sa.85. Gene Therapy for Purine Nucleoside Phosphorylase Deficiency","year":2006,"lang":"en","type":"article","venue":"Clinical Immunology","topic":"Biochemical and Molecular Research","field":"Biochemistry, Genetics and Molecular Biology","cited_by":0,"is_retracted":false,"has_abstract":false,"ca_institutions":"Hospital for Sick Children","funders":"","keywords":"Purine nucleoside phosphorylase; Purine; Genetic enhancement; Nucleoside; Glycogen phosphorylase; Gene; Medicine; Chemistry; Biochemistry; Enzyme","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0001733338,0.0003733711,0.0004128141,0.0006902395,0.0002204751,0.000251605,0.0002825575,0.0006095073,0.003895335],"category_scores_gemma":[0.0001723558,0.000115353,0.0003603497,0.0003633212,0.0003071469,0.0001837124,0.0002233103,0.0008623641,0.001639143],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0001472439,"about_ca_system_score_gemma":0.0002596118,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.0005139346,"about_ca_topic_score_gemma":0.0004045746,"domain_scores_codex":[0.9998894,0.00002516056,0.000006235484,0.00001712231,0.00002963072,0.00003242934],"domain_scores_gemma":[0.9999359,0.00001666229,0.00001313012,0.000006677859,0.000005242652,0.00002239715],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"bench_or_experimental","study_design_gemma":"not_applicable","study_design_scores_codex":[0.003586409,0.0008423621,0.001248186,0.0003854583,0.0001274948,0.001080829,0.0001136517,0.001362241,0.8218412,0.00818844,0.004814727,0.156409],"study_design_scores_gemma":[0.001363584,0.009060357,0.01579445,0.0001656364,0.0003878012,0.006317194,0.0000552758,0.00428743,0.8096723,0.002181645,0.1506704,0.00004400134],"study_design_candidate":"not_applicable","study_design_consensus":null,"genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.8014762,0.03339538,0.02710306,0.003099393,0.001607342,0.0004259545,0.001826922,0.001715318,0.1293505],"genre_scores_gemma":[0.9490368,0.005844655,0.007652249,0.0005322811,0.0001930102,0.0001438146,0.000754463,0.00009522686,0.03574741],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.003895335,"threshold_uncertainty_score":0.01303124,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.02758294791157592,"score_gpt":0.3433982590196939,"score_spread":0.315815311108118,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}