{"id":"W2062718003","doi":"10.1016/j.bbmt.2014.06.019","title":"Outcomes after Hematopoietic Stem Cell Transplantation for Children with I-Cell Disease","year":2014,"lang":"en","type":"article","venue":"Biology of Blood and Marrow Transplantation","topic":"Lysosomal Storage Disorders Research","field":"Medicine","cited_by":35,"is_retracted":false,"has_abstract":true,"ca_institutions":"Alberta Children's Hospital; BC Children's Hospital; University of British Columbia","funders":"National Cancer Institute; Office of Naval Research; National Heart, Lung, and Blood Institute; Terumo BCT; Health Resources and Services Administration; Medac; Swedish Orphan Biovitrum; Otsuka America; Incyte; Genentech; Seattle Genetics; Chimerix; Medical College of Wisconsin; Blue Cross and Blue Shield Association; Takeda Oncology; University of Minnesota; Kiadis Pharma; Sigma-Tau Pharmaceuticals; Therakos; StemCyte; Tarix Pharmaceuticals; University of Utah; HistoGenetics; WellPoint; Teva Pharmaceutical Industries; National Marrow Donor Program; St. Baldrick's Foundation; National Institute of Allergy and Infectious Diseases; Roswell Park Cancer Institute; Fred Hutchinson Cancer Research Center; Health Research; U.S. Navy; Celgene; Osiris Therapeutics; Merck; GlaxoSmithKline; Leukemia and Lymphoma Society; Be The Match Foundation; Allos Therapeutics; Actinium Pharmaceuticals; Ariad Pharmaceuticals; Otsuka America Pharmaceutical; Amgen; Onyx Pharmaceuticals; U.S. Department of Defense; Sanofi","keywords":"Medicine; Hematopoietic stem cell transplantation; Disease; Stem cell; Transplantation; Lysosomal storage disease; Hematopoietic stem cell; Cause of death; Haematopoiesis; Pediatrics; Intensive care medicine; Internal medicine; Surgery","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0003509111,0.0002569734,0.000390465,0.0003764604,0.0006332,0.00051804,0.0002168569,0.0003349236,0.001076553],"category_scores_gemma":[0.001431544,0.0000565603,0.0004821727,0.0005269063,0.0004056057,0.0003475729,0.0006073973,0.0008114437,0.0001541479],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0007052422,"about_ca_system_score_gemma":0.0005683229,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.001571395,"about_ca_topic_score_gemma":0.002666783,"domain_scores_codex":[0.9997185,0.00004438051,0.00002709575,0.00002902628,0.00007167499,0.0001094444],"domain_scores_gemma":[0.9987804,0.0001747448,0.0004618685,0.00004108174,0.00007389618,0.0004679562],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"observational","study_design_gemma":"observational","study_design_scores_codex":[0.0007727361,0.0001670524,0.9454994,0.0001100961,0.0001451001,0.01407981,0.0005149302,0.0004342091,0.0008878667,0.0004495158,0.001804009,0.03513527],"study_design_scores_gemma":[0.00007048175,0.001967287,0.9479132,0.000161672,0.0002022916,0.04317674,0.000796227,0.0003750545,0.0009928124,0.0006131119,0.003703386,0.00002777069],"study_design_candidate":"observational","study_design_consensus":"observational","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9935204,0.002912041,0.000241409,0.0003982091,0.00006211145,0.00001883331,0.0004535877,0.00002008106,0.002373327],"genre_scores_gemma":[0.9979596,0.0008602829,0.00006954466,0.000115224,0.0000379656,0.0000100531,0.0007270193,0.000004982954,0.000215319],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.001571395,"threshold_uncertainty_score":0.00511694,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.007750355377629409,"score_gpt":0.2396496988129569,"score_spread":0.2318993434353274,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}