{"id":"W2079150340","doi":"10.1152/ajplung.00117.2004","title":"Therapeutic gene transfer to dystrophic diaphragm by an adenoviral vector deleted of all viral genes","year":2004,"lang":"en","type":"article","venue":"American Journal of Physiology-Lung Cellular and Molecular Physiology","topic":"Muscle Physiology and Disorders","field":"Biochemistry, Genetics and Molecular Biology","cited_by":29,"is_retracted":false,"has_abstract":true,"ca_institutions":"Royal Victoria Hospital","funders":"","keywords":"Dystrophin; Duchenne muscular dystrophy; Viral vector; Biology; mdx mouse; Sarcolemma; Genetic enhancement; Muscular dystrophy; Transgene; Utrophin; Diaphragm (acoustics); Gene; Cell biology; Molecular biology; Myocyte; Genetics","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0002795297,0.0006103718,0.0005282701,0.0003683011,0.0001607083,0.0003878026,0.0003727274,0.0006959799,0.001023086],"category_scores_gemma":[0.0001701967,0.0002037713,0.0003657711,0.0001671297,0.0003678455,0.0002954192,0.0002513856,0.0009596125,0.000304033],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0002848407,"about_ca_system_score_gemma":0.0003020926,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.000450617,"about_ca_topic_score_gemma":0.0006029845,"domain_scores_codex":[0.9997465,0.00004101276,0.00002543921,0.00006827034,0.00005988392,0.00005898127],"domain_scores_gemma":[0.9998573,0.00003354114,0.00004615559,0.00001830433,0.00001124583,0.00003353774],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"bench_or_experimental","study_design_gemma":"bench_or_experimental","study_design_scores_codex":[0.00006212189,0.00006076589,0.00004566777,0.00004580088,0.000005444373,0.00003653372,0.00001420665,0.00007306059,0.998024,0.0001435406,0.00003332345,0.001455595],"study_design_scores_gemma":[0.00008188585,0.001975306,0.0011804,0.00001692092,0.00003835033,0.0004214949,0.00002101311,0.001346519,0.9913947,0.00005499386,0.00346153,0.000006948121],"study_design_candidate":"bench_or_experimental","study_design_consensus":"bench_or_experimental","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9698238,0.004065366,0.02242006,0.0002165713,0.0002215862,0.0004024577,0.000540044,0.000400425,0.001909715],"genre_scores_gemma":[0.9712642,0.002907782,0.01951288,0.000119388,0.0000518429,0.0002729011,0.0009493806,0.00006551588,0.004856043],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.001023086,"threshold_uncertainty_score":0.003422558,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.004174580131427714,"score_gpt":0.2257697123333649,"score_spread":0.2215951322019372,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}