{"id":"W2079150340","doi":"10.1152/ajplung.00117.2004","title":"Therapeutic gene transfer to dystrophic diaphragm by an adenoviral vector deleted of all viral genes","year":2004,"lang":"en","type":"article","venue":"American Journal of Physiology-Lung Cellular and Molecular Physiology","topic":"Muscle Physiology and Disorders","field":"Biochemistry, Genetics and Molecular Biology","cited_by":29,"is_retracted":false,"has_abstract":true,"ca_institutions":"Royal Victoria Hospital","funders":"","keywords":"Dystrophin; Duchenne muscular dystrophy; Viral vector; Biology; mdx mouse; Sarcolemma; Genetic enhancement; Muscular dystrophy; Transgene; Utrophin; Diaphragm (acoustics); Gene; Cell biology; Molecular biology; Myocyte; Genetics","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"codex-gemma-dda1882f352a","candidate_categories":["metaepi_narrow"],"consensus_categories":[],"category_scores_codex":[0.0001714879,0.0004146649,0.0008268827,0.0001471249,0.00008529062,0.000008465221,0.0004879577,0.0002271422,0.00001612683],"category_scores_gemma":[0.00002320252,0.0003683429,0.0003304291,0.000184665,0.0008348522,0.00001947918,0.0001014368,0.0002847959,0.000002500846],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.00002090836,"about_ca_system_score_gemma":0.0001468275,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.00008502425,"about_ca_topic_score_gemma":0.000005126915,"domain_scores_codex":[0.9976473,0.0004394556,0.0005992861,0.0005987323,0.0001609464,0.0005543027],"domain_scores_gemma":[0.9987744,0.00002379705,0.0002443075,0.0004761336,0.0001882731,0.0002930589],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"bench_or_experimental","study_design_gemma":"bench_or_experimental","study_design_scores_codex":[0.001619814,0.000334139,0.00004465387,0.00002996678,0.0005394509,0.000009170812,0.0001689535,0.00205276,0.9936627,0.0002334185,0.00004336751,0.001261607],"study_design_scores_gemma":[0.001701634,0.007994251,0.006491561,0.00001551476,0.0001729576,0.00004902881,0.0001615206,0.00003236923,0.9815813,0.0008524525,0.0005239728,0.0004234918],"study_design_candidate":"bench_or_experimental","study_design_consensus":"bench_or_experimental","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9873713,0.003772173,0.008192241,0.0002241088,0.0001576481,0.0002223581,0.00004024398,0.00001027121,0.00000966378],"genre_scores_gemma":[0.9964721,0.0005383554,0.0007162907,0.001820783,0.0001911663,0.00001519385,0.0001850974,0.00005635727,0.000004678604],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.01208145,"threshold_uncertainty_score":0.9998769,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.004174580131427714,"score_gpt":0.2257697123333649,"score_spread":0.2215951322019372,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}