{"id":"W2092931860","doi":"10.1038/mt.2011.254","title":"Gene Transfer Using HACs: A Key Step Closer to Ex Vivo Gene Therapy Using Autologous Gene–Corrected Cells to Treat Muscular Dystrophy","year":2011,"lang":"en","type":"article","venue":"Molecular Therapy","topic":"Muscle Physiology and Disorders","field":"Biochemistry, Genetics and Molecular Biology","cited_by":1,"is_retracted":false,"has_abstract":true,"ca_institutions":"Université Laval","funders":"","keywords":"Ex vivo; Genetic enhancement; Muscular dystrophy; Gene transfer; Gene; Biology; In vivo; Genetics; Medicine","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"codex-gemma-dda1882f352a","candidate_categories":["metaepi_narrow"],"consensus_categories":[],"category_scores_codex":[0.0001648183,0.0006318349,0.0005333556,0.0001924577,0.0002172479,0.0000393507,0.0005393609,0.0004673594,0.0001930635],"category_scores_gemma":[0.00001091258,0.0005972577,0.0004159281,0.0003596507,0.0001176159,0.00001164932,0.00009194947,0.0001692474,0.00003581604],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.00004630213,"about_ca_system_score_gemma":0.0001345892,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.0004354533,"about_ca_topic_score_gemma":0.00001853697,"domain_scores_codex":[0.9970336,0.0003519377,0.0004419842,0.001104768,0.0002481278,0.0008196003],"domain_scores_gemma":[0.9983457,0.000008450407,0.00007357603,0.00105707,0.0001723568,0.0003428764],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"bench_or_experimental","study_design_gemma":"bench_or_experimental","study_design_scores_codex":[0.001884821,0.000324956,0.0001094356,0.00000820746,0.000317906,0.00008076511,0.0007229431,0.002323025,0.9880514,0.000009404843,0.00007169311,0.006095419],"study_design_scores_gemma":[0.002173027,0.001352471,0.0006094298,0.00001120441,0.00005141278,0.00003681171,0.00005781213,0.0002954853,0.9914476,0.00005550007,0.003164454,0.0007448467],"study_design_candidate":"bench_or_experimental","study_design_consensus":"bench_or_experimental","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.8918577,0.002282523,0.1042484,0.00003694086,0.0003157935,0.0009933871,0.00005077159,0.00006032606,0.0001540897],"genre_scores_gemma":[0.9705386,0.0005340594,0.02460293,0.00371105,0.000188297,0.00008022523,0.00008201943,0.0001678838,0.00009497046],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.07964551,"threshold_uncertainty_score":0.9996479,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.02637595910608162,"score_gpt":0.2484050853653499,"score_spread":0.2220291262592682,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}