{"id":"W2092931860","doi":"10.1038/mt.2011.254","title":"Gene Transfer Using HACs: A Key Step Closer to Ex Vivo Gene Therapy Using Autologous Gene–Corrected Cells to Treat Muscular Dystrophy","year":2011,"lang":"en","type":"article","venue":"Molecular Therapy","topic":"Muscle Physiology and Disorders","field":"Biochemistry, Genetics and Molecular Biology","cited_by":1,"is_retracted":false,"has_abstract":true,"ca_institutions":"Université Laval","funders":"","keywords":"Ex vivo; Genetic enhancement; Muscular dystrophy; Gene transfer; Gene; Biology; In vivo; Genetics; Medicine","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.001661637,0.000557681,0.001116,0.0008899469,0.0003595083,0.002497882,0.0008187891,0.001361788,0.005535632],"category_scores_gemma":[0.001042715,0.000286145,0.0007724848,0.0005559929,0.001056331,0.002302169,0.0008716792,0.006165859,0.001862553],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0005838374,"about_ca_system_score_gemma":0.0007816665,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.0007431609,"about_ca_topic_score_gemma":0.001101288,"domain_scores_codex":[0.9993829,0.0001670172,0.00004469405,0.00008779534,0.0002342071,0.00008346962],"domain_scores_gemma":[0.9994319,0.0002277193,0.00005028972,0.00009443083,0.000136382,0.00005924464],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"design_other","study_design_gemma":"bench_or_experimental","study_design_scores_codex":[0.001082897,0.001386118,0.0008600298,0.005700217,0.0004133307,0.001324599,0.00134029,0.001356025,0.4237117,0.05033219,0.05796512,0.4545276],"study_design_scores_gemma":[0.0004932132,0.002830475,0.001782062,0.001127051,0.0003616787,0.002740718,0.0006042347,0.001901787,0.2511364,0.01325196,0.7236735,0.00009678484],"study_design_candidate":"bench_or_experimental","study_design_consensus":null,"genre_codex":"review","genre_gemma":"empirical","genre_scores_codex":[0.1391514,0.4637099,0.2262054,0.08680885,0.02267777,0.002069592,0.002324894,0.002190669,0.05486155],"genre_scores_gemma":[0.3740936,0.4233719,0.1247938,0.02910196,0.006135952,0.001596383,0.002499392,0.0009096594,0.03749749],"genre_candidate":"empirical","genre_consensus":null,"teacher_disagreement_score":0.005535632,"threshold_uncertainty_score":0.01851851,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.02637595910608162,"score_gpt":0.2484050853653499,"score_spread":0.2220291262592682,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}