{"id":"W2109581185","doi":"10.1542/peds.113.5.e448","title":"Long-Term Intravenous Treatment of Pompe Disease With Recombinant Human α-Glucosidase From Milk","year":2004,"lang":"en","type":"article","venue":"PEDIATRICS","topic":"Lysosomal Storage Disorders Research","field":"Medicine","cited_by":354,"is_retracted":false,"has_abstract":true,"ca_institutions":"","funders":"Fondation pour la Recherche Médicale","keywords":"Medicine; Disease; Recombinant DNA; Enzyme replacement therapy; Pediatrics; Internal medicine; Gene; Biochemistry","routes":{"ca_aff":false,"ca_fund":false,"ca_venue":false,"about_ca":true,"invisible_to_affiliation_only":true},"retraction":null,"screen":null,"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.02197907818458139,"score_gpt":0.2916702128781607,"score_spread":0.2696911346935793,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}