{"id":"W2112523289","doi":"10.1016/j.ymthe.2003.11.023","title":"Dystrophin Expression in Myofibers of Duchenne Muscular Dystrophy Patients Following Intramuscular Injections of Normal Myogenic Cells","year":2004,"lang":"en","type":"article","venue":"Molecular Therapy","topic":"Muscle Physiology and Disorders","field":"Biochemistry, Genetics and Molecular Biology","cited_by":193,"is_retracted":false,"has_abstract":false,"ca_institutions":"Hôtel-Dieu de Québec; Hôpital de l'Enfant-Jésus; Université Laval; SNC-Lavalin (Canada)","funders":"","keywords":"Dystrophin; Duchenne muscular dystrophy; Muscular dystrophy; Exon; Biology; Immunosuppression; Molecular biology; Skeletal muscle; Medicine; Internal medicine; Endocrinology; Immunology; Gene; Genetics","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"codex-gemma-dda1882f352a","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0001238449,0.0002186631,0.0002878614,0.0001334298,0.00004821281,0.000005093566,0.0002449648,0.0002237618,0.0000136527],"category_scores_gemma":[0.00002591775,0.0002147284,0.0003646908,0.0002289472,0.0001140913,0.00001039968,0.00006700357,0.0001274383,0.000002200513],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.00002094459,"about_ca_system_score_gemma":0.00007376277,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.00009537169,"about_ca_topic_score_gemma":0.000008683853,"domain_scores_codex":[0.9986358,0.0001228307,0.0003913682,0.000369063,0.0001935891,0.0002873198],"domain_scores_gemma":[0.9992314,0.000006239329,0.0001567151,0.0004616929,0.00007864677,0.00006529556],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"bench_or_experimental","study_design_gemma":"bench_or_experimental","study_design_scores_codex":[0.000316146,0.0004591747,0.001498269,0.00002127114,0.0001267485,0.000006844183,0.0001453167,0.008968831,0.9877328,0.00004178224,0.000007575,0.0006752466],"study_design_scores_gemma":[0.003781619,0.0008049489,0.008592371,0.00003707729,0.00001747873,8.332895e-7,0.00007167472,0.000006864625,0.9859505,0.0003140216,0.0002144666,0.0002081124],"study_design_candidate":"bench_or_experimental","study_design_consensus":"bench_or_experimental","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9948332,0.0009432033,0.003628308,0.0000214325,0.0001603887,0.0003235347,0.00001220258,0.000008398182,0.0000692802],"genre_scores_gemma":[0.9980934,0.0001917583,0.001428777,0.00009179502,0.00002168759,0.00003135898,0.0001034978,0.00003226477,0.00000552173],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.008961966,"threshold_uncertainty_score":0.8756369,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.003271101709141726,"score_gpt":0.2072330217986358,"score_spread":0.2039619200894941,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}