{"id":"W2119182840","doi":"10.1177/1073858410386236","title":"Gene Therapy in Mouse Models of Huntington Disease","year":2011,"lang":"en","type":"review","venue":"The Neuroscientist","topic":"Genetic Neurodegenerative Diseases","field":"Neuroscience","cited_by":20,"is_retracted":false,"has_abstract":true,"ca_institutions":"University of British Columbia","funders":"National Institute of Neurological Disorders and Stroke; Hereditary Disease Foundation","keywords":"Neuropathology; Huntingtin; Huntington's disease; Disease; Neuroscience; Huntingtin Protein; Biology; Gene knockin; Psychology; Bioinformatics; Medicine; Gene; Genetics; Pathology","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"codex-gemma-dda1882f352a","candidate_categories":["metaepi_narrow"],"consensus_categories":[],"category_scores_codex":[0.0002932963,0.0005901676,0.001050578,0.0003734489,0.0001978516,0.0001068992,0.002019465,0.00008414973,0.00004942824],"category_scores_gemma":[0.0005471776,0.0003953702,0.00054804,0.001092979,0.000710918,0.0001507472,0.0004447577,0.0003944614,0.00005812101],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.00003223329,"about_ca_system_score_gemma":0.000308523,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.00002231354,"about_ca_topic_score_gemma":0.000004119675,"domain_scores_codex":[0.995411,0.00133873,0.0008358011,0.001270128,0.0005714205,0.0005728694],"domain_scores_gemma":[0.9971786,0.0003409989,0.0006219868,0.001590286,0.00004746233,0.0002206833],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"design_other","study_design_gemma":"not_applicable","study_design_scores_codex":[0.0002668289,0.004108516,0.00006868289,0.009349255,0.00003350936,0.0001593066,0.0005560987,0.0008453247,0.1486814,0.01117073,0.001304989,0.8234554],"study_design_scores_gemma":[0.0009656855,0.0002821632,0.0001378408,0.001912759,0.00034505,0.00002233588,0.000005240899,0.0003302909,0.4374952,0.001738008,0.5552335,0.001531936],"study_design_candidate":"design_other","study_design_consensus":null,"genre_codex":"review","genre_gemma":"review","genre_scores_codex":[0.03434903,0.9602871,0.00003869116,0.00001939336,0.001464976,0.002319192,0.000829951,0.00008716026,0.0006044916],"genre_scores_gemma":[0.008584897,0.9887262,0.00001631921,0.0003065603,0.00006425117,0.0001952234,0.00001164033,0.000123974,0.001970919],"genre_candidate":"review","genre_consensus":"review","teacher_disagreement_score":0.8219234,"threshold_uncertainty_score":0.9998498,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.1397249982109157,"score_gpt":0.3287872058894811,"score_spread":0.1890622076785654,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}