{"id":"W2119607462","doi":"10.1186/1750-1172-9-5","title":"Intra-Erythrocyte Infusion of Dexamethasone Reduces Neurological Symptoms in Ataxia Teleangiectasia Patients: Results of a Phase 2 Trial","year":2014,"lang":"en","type":"article","venue":"Orphanet Journal of Rare Diseases","topic":"Genetic Neurodegenerative Diseases","field":"Neuroscience","cited_by":142,"is_retracted":false,"has_abstract":true,"ca_institutions":"","funders":"Ontario Institute for Regenerative Medicine","keywords":"Medicine; Tolerability; Ataxia; Dexamethasone; Population; Dosing; Internal medicine; Adverse effect; Anesthesia","routes":{"ca_aff":false,"ca_fund":true,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":true},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"codex-gemma-dda1882f352a","candidate_categories":["metaresearch"],"consensus_categories":[],"category_scores_codex":[0.0003157025,0.0002925577,0.0007435229,0.0004277673,0.00005715918,0.00003063205,0.0006083029,0.00008450051,0.00009263241],"category_scores_gemma":[0.01144839,0.0002307315,0.0002827058,0.0005763061,0.0003535588,0.0002813685,0.0001325186,0.0002330122,0.000003475509],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.00002390823,"about_ca_system_score_gemma":0.0001942602,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.000007068352,"about_ca_topic_score_gemma":0.000002345056,"domain_scores_codex":[0.9956837,0.00120254,0.001443055,0.0004451236,0.0008816863,0.0003438636],"domain_scores_gemma":[0.9963028,0.001162513,0.001531963,0.000360987,0.000331623,0.0003100691],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"bench_or_experimental","study_design_gemma":"bench_or_experimental","study_design_scores_codex":[0.2044593,0.01288064,0.02843622,0.0001636559,0.0000561734,0.0002887778,0.0004373119,0.001340332,0.7020299,0.00007572876,0.00207706,0.04775492],"study_design_scores_gemma":[0.09703724,0.01707036,0.05746052,0.0002464834,0.0002115033,0.00004199653,0.00005350903,0.0003706876,0.8264933,0.0002759738,0.000387108,0.0003512674],"study_design_candidate":"bench_or_experimental","study_design_consensus":"bench_or_experimental","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9981158,0.0003331716,0.00003810814,0.0000845157,0.0004478533,0.0004523109,0.0004720592,0.00001442808,0.00004178386],"genre_scores_gemma":[0.9992321,0.0001760913,0.0001405249,0.0001990683,0.0001873023,0.00000882844,0.00002317031,0.00002506429,0.000007865246],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.1244634,"threshold_uncertainty_score":0.9968786,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.02039683248315424,"score_gpt":0.2796798601809671,"score_spread":0.2592830276978129,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}