{"id":"W2511785149","doi":"10.1212/wnl.86.16_supplement.p3.164","title":"Safety and Tolerability of Ataluren in a Phase 3 Study of Patients with Nonsense Mutation Duchenne Muscular Dystrophy (P3.164)","year":2016,"lang":"en","type":"article","venue":"Neurology","topic":"Muscle Physiology and Disorders","field":"Biochemistry, Genetics and Molecular Biology","cited_by":2,"is_retracted":false,"has_abstract":true,"ca_institutions":"London Health Sciences Centre; Western University","funders":"","keywords":"Duchenne muscular dystrophy; Tolerability; Nonsense mutation; Medicine; Muscular dystrophy; Nonsense; Mutation; Pediatrics; Internal medicine; Genetics; Adverse effect; Missense mutation; Biology","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.002579911,0.0008446882,0.00169382,0.0002459649,0.0003811607,0.0006107728,0.0006333007,0.0008231406,0.002147744],"category_scores_gemma":[0.001235269,0.0003503665,0.001267311,0.0002224399,0.0004778803,0.0005756941,0.0002384376,0.001630793,0.0004684584],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0004646046,"about_ca_system_score_gemma":0.000757315,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.0004772393,"about_ca_topic_score_gemma":0.001580889,"domain_scores_codex":[0.9990754,0.0006326622,0.00005054894,0.00009169726,0.00007752689,0.0000722342],"domain_scores_gemma":[0.9990084,0.0002511516,0.0003131336,0.00006684603,0.00006732439,0.0002932636],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"randomized_trial","study_design_gemma":"randomized_trial","study_design_scores_codex":[0.790745,0.03660381,0.0150863,0.001173779,0.002448461,0.0004885994,0.0004447096,0.001149093,0.04159594,0.0001485377,0.002249048,0.1078667],"study_design_scores_gemma":[0.4859444,0.4720301,0.03527838,0.00005719765,0.0008386909,0.0004985047,0.00008265986,0.0007725613,0.002893586,0.00009356161,0.001473922,0.00003643861],"study_design_candidate":"randomized_trial","study_design_consensus":"randomized_trial","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.996012,0.002061635,0.0002672743,0.0001241542,0.00003480793,0.0005627756,0.000327167,0.00004209829,0.0005680045],"genre_scores_gemma":[0.9964325,0.0009132553,0.0006975164,0.0003352801,0.00006499727,0.0006090166,0.0004848304,0.00001059123,0.0004519922],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.002579911,"threshold_uncertainty_score":0.01364404,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.004181378004724554,"score_gpt":0.22383496625164,"score_spread":0.2196535882469154,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}