{"id":"W2584067066","doi":"","title":"Ocular Gene Therapy for Choroideremia: the Alberta Experience","year":2016,"lang":"en","type":"article","venue":"","topic":"Retinal Development and Disorders","field":"Biochemistry, Genetics and Molecular Biology","cited_by":2,"is_retracted":false,"has_abstract":false,"ca_institutions":"University of Alberta","funders":"","keywords":"Choroideremia; Genetic enhancement; Medicine; Ophthalmology; Gene; Biology; Genetics; Retinal","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":true,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.001693273,0.0004976518,0.0003140269,0.0007743425,0.0009740127,0.001254459,0.0006582309,0.0009060947,0.004503199],"category_scores_gemma":[0.001004817,0.000130496,0.0002291732,0.0009001023,0.001276352,0.0005126638,0.0006709388,0.001139579,0.0005076184],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.004419962,"about_ca_system_score_gemma":0.005338458,"about_ca_topic_candidate":true,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.1534456,"about_ca_topic_score_gemma":0.338584,"domain_scores_codex":[0.9996523,0.00008276625,0.00001180263,0.00003594518,0.0001573711,0.00005982496],"domain_scores_gemma":[0.9995154,0.0001615487,0.00002925553,0.00003047721,0.0001212062,0.0001420497],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"design_other","study_design_gemma":"observational","study_design_scores_codex":[0.002027234,0.001466495,0.01412007,0.0003265064,0.000143854,0.008828055,0.001531514,0.002190304,0.01988649,0.02385701,0.04046682,0.8851557],"study_design_scores_gemma":[0.001712044,0.003828012,0.08151376,0.0009956232,0.0004343859,0.02586533,0.002170025,0.002369491,0.01973695,0.01178257,0.8493854,0.0002064895],"study_design_candidate":"observational","study_design_consensus":null,"genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.3798698,0.2260396,0.0120242,0.03966903,0.002599882,0.0001755152,0.0005604197,0.0002820443,0.3387795],"genre_scores_gemma":[0.668349,0.2579855,0.01291333,0.006236652,0.001148066,0.0000635773,0.0004262293,0.000234457,0.05264311],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.8465544,"threshold_uncertainty_score":0.3051049,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.01004171423334654,"score_gpt":0.2488316961953958,"score_spread":0.2387899819620493,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}