{"id":"W2748665139","doi":"10.1002/mus.25776","title":"Clinical trial of L‐Carnitine and valproic acid in spinal muscular atrophy type I","year":2017,"lang":"en","type":"article","venue":"Muscle & Nerve","topic":"Neurogenetic and Muscular Disorders Research","field":"Medicine","cited_by":29,"is_retracted":false,"has_abstract":true,"ca_institutions":"University of Manitoba; Centre Hospitalier Universitaire Sainte-Justine","funders":"Eunice Kennedy Shriver National Institute of Child Health and Human Development; Cure SMA","keywords":"Valproic Acid; Spinal muscular atrophy; Medicine; SMA*; Adverse effect; Carnitine; Compound muscle action potential; Clinical trial; Retrospective cohort study; Internal medicine; Pediatrics; Anesthesia; Surgery; Epilepsy","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"codex-gemma-dda1882f352a","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0006484674,0.000116915,0.000409629,0.00009217071,0.00008019478,0.00002464425,0.0001782723,0.0001102665,0.00006831696],"category_scores_gemma":[0.0007879267,0.0001004247,0.0001772039,0.00008599334,0.0002463724,0.00004523773,0.0001645177,0.0003001485,0.00001530447],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.00001060705,"about_ca_system_score_gemma":0.0001225491,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.0001455775,"about_ca_topic_score_gemma":0.00002959627,"domain_scores_codex":[0.9985887,0.0001288541,0.0003914791,0.0003193286,0.0003199838,0.0002516399],"domain_scores_gemma":[0.9989054,0.00002931135,0.0001237097,0.0006798762,0.0001067528,0.000154958],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"design_other","study_design_gemma":"observational","study_design_scores_codex":[0.04137595,0.001728907,0.1655835,0.0005227014,0.0001968797,0.0007813598,0.0001546865,0.000001431349,0.03690523,0.0003307113,0.0002917908,0.7521269],"study_design_scores_gemma":[0.05669806,0.004985544,0.9309173,0.0001152693,0.00008564108,0.00001723935,0.00005320997,0.00008624661,0.001060674,0.0001443067,0.00570961,0.0001269521],"study_design_candidate":"observational","study_design_consensus":null,"genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9957356,0.001070545,0.00001545268,0.0005781658,0.0002076028,0.0006170036,0.0000020141,0.00001052371,0.001763083],"genre_scores_gemma":[0.998619,0.0005467176,0.0002980784,0.00006768438,0.0002497611,0.00001516098,0.000005498752,0.00002107315,0.0001770758],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.7653338,"threshold_uncertainty_score":0.4095202,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.09515227669070062,"score_gpt":0.4189088194222325,"score_spread":0.3237565427315319,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}