{"id":"W2748665139","doi":"10.1002/mus.25776","title":"Clinical trial of L‐Carnitine and valproic acid in spinal muscular atrophy type I","year":2017,"lang":"en","type":"article","venue":"Muscle & Nerve","topic":"Neurogenetic and Muscular Disorders Research","field":"Medicine","cited_by":29,"is_retracted":false,"has_abstract":true,"ca_institutions":"University of Manitoba; Centre Hospitalier Universitaire Sainte-Justine","funders":"Eunice Kennedy Shriver National Institute of Child Health and Human Development; Cure SMA","keywords":"Valproic Acid; Spinal muscular atrophy; Medicine; SMA*; Adverse effect; Carnitine; Compound muscle action potential; Clinical trial; Retrospective cohort study; Internal medicine; Pediatrics; Anesthesia; Surgery; Epilepsy","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.001712899,0.000630903,0.001573224,0.0002450952,0.0003353095,0.0006219871,0.0006636743,0.001003888,0.00239231],"category_scores_gemma":[0.001741534,0.000231174,0.0006576139,0.0002520935,0.0005528782,0.0004266711,0.0003119647,0.001444457,0.0003352773],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0006808239,"about_ca_system_score_gemma":0.001332917,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.0003650366,"about_ca_topic_score_gemma":0.0009686683,"domain_scores_codex":[0.9991993,0.0004936157,0.00007671478,0.00009626099,0.00006029963,0.00007387304],"domain_scores_gemma":[0.9989052,0.0003302256,0.0002838639,0.00005523795,0.00008787095,0.0003375319],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"randomized_trial","study_design_gemma":"nonrandomized_trial","study_design_scores_codex":[0.892651,0.01366346,0.007174888,0.001451131,0.001210729,0.0004062285,0.0001961955,0.0005160513,0.01650902,0.0001974804,0.0009759648,0.06504783],"study_design_scores_gemma":[0.4062963,0.5781832,0.0083907,0.0001323724,0.0004944832,0.0004184212,0.00005700145,0.0003738888,0.003347186,0.0001044054,0.002188358,0.00001365135],"study_design_candidate":"nonrandomized_trial","study_design_consensus":null,"genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9893683,0.007618006,0.0001869297,0.0003677929,0.0001067667,0.001090209,0.0002897771,0.00001385872,0.0009584356],"genre_scores_gemma":[0.9935602,0.002226435,0.0007060129,0.0005042698,0.0002266191,0.001483098,0.0005990968,0.00000509731,0.0006891637],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.00239231,"threshold_uncertainty_score":0.009058833,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.09515227669070062,"score_gpt":0.4189088194222325,"score_spread":0.3237565427315319,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}