{"id":"W2810713430","doi":"10.1017/cjn.2018.178","title":"P.076 Safety of Eteplirsen, a phosphorodiamidate morpholino oligomer, in Duchenne Muscular Dystrophy patients amenable to Exon 51 skipping","year":2018,"lang":"en","type":"article","venue":"Canadian Journal of Neurological Sciences / Journal Canadien des Sciences Neurologiques","topic":"Muscle Physiology and Disorders","field":"Biochemistry, Genetics and Molecular Biology","cited_by":0,"is_retracted":false,"has_abstract":true,"ca_institutions":"Calgary Laboratory Services","funders":"","keywords":"Medicine; Duchenne muscular dystrophy; Rash; Adverse effect; Muscular dystrophy; Tolerability; Dermatology; Internal medicine; Pediatrics","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":true,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0004811947,0.0001797599,0.0003174434,0.00009821303,0.0001321078,0.0004166337,0.0001873771,0.0004829791,0.005165513],"category_scores_gemma":[0.0008918781,0.00007377501,0.0004856314,0.0001239944,0.0002065983,0.000249883,0.000127715,0.0008716115,0.001033593],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0002201166,"about_ca_system_score_gemma":0.0002999922,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.0001596901,"about_ca_topic_score_gemma":0.0001758775,"domain_scores_codex":[0.999833,0.00007515295,0.00001808868,0.00002234369,0.00003663427,0.00001477856],"domain_scores_gemma":[0.9995239,0.0001594636,0.000160962,0.00001865198,0.00004816438,0.00008894866],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"design_other","study_design_gemma":"observational","study_design_scores_codex":[0.2304207,0.006548715,0.03726109,0.002772557,0.001093059,0.003363929,0.0003902898,0.002587711,0.07545853,0.001175842,0.02394767,0.6149799],"study_design_scores_gemma":[0.09024084,0.6169893,0.1281295,0.001045122,0.001360488,0.01424773,0.0002916812,0.006995121,0.05029947,0.001223722,0.08910267,0.00007442906],"study_design_candidate":"observational","study_design_consensus":null,"genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9718393,0.01369506,0.0006618224,0.001219762,0.0003142468,0.000252952,0.001461341,0.0001262973,0.01042929],"genre_scores_gemma":[0.993502,0.002586837,0.0003359185,0.0006292714,0.0001546062,0.0001244421,0.0006978072,0.0000145329,0.001954686],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.005165513,"threshold_uncertainty_score":0.0172804,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.01329668932788412,"score_gpt":0.2427821057439365,"score_spread":0.2294854164160524,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}