{"id":"W2884962542","doi":"10.1017/cjn.2018.59","title":"Response to the Canadian Agency for Drugs and Technologies in Health and Institut national d’excellence en santé et en services sociaux decision regarding nusinersen for Spinal Muscular Atrophy","year":2018,"lang":"en","type":"article","venue":"Canadian Journal of Neurological Sciences / Journal Canadien des Sciences Neurologiques","topic":"Neurogenetic and Muscular Disorders Research","field":"Medicine","cited_by":1,"is_retracted":false,"has_abstract":true,"ca_institutions":"Agricultural Research Institute of Ontario; Hospital for Sick Children; University of Ottawa; McGill University; University of Calgary; Children's Hospital of Western Ontario; Children's Hospital of Eastern Ontario; Montreal Neurological Institute and Hospital; SickKids Foundation; Western University; University of Toronto; BC Children's Hospital; London Health Sciences Centre","funders":"","keywords":"Excellence; Agency (philosophy); Spinal muscular atrophy; Medicine; Political science; Family medicine; Sociology; Internal medicine; Disease; Law","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":true,"about_ca":true,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0150785,0.001633317,0.004145249,0.003182697,0.012993,0.008287682,0.007996183,0.1168199,0.03598639],"category_scores_gemma":[0.07170998,0.00223807,0.006550001,0.002778307,0.005670233,0.002912577,0.004314293,0.05519845,0.0161922],"about_ca_system_candidate":true,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.05121277,"about_ca_system_score_gemma":0.1778716,"about_ca_topic_candidate":true,"about_ca_topic_consensus":true,"about_ca_topic_score_codex":0.6375004,"about_ca_topic_score_gemma":0.8508751,"domain_scores_codex":[0.9613235,0.002071147,0.003681442,0.002315306,0.02321873,0.007389859],"domain_scores_gemma":[0.9352454,0.008639908,0.002477741,0.00132085,0.03722506,0.01509102],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"not_applicable","study_design_gemma":"not_applicable","study_design_scores_codex":[0.00005559536,0.00002914582,0.0002507044,0.00005093385,0.00002017844,0.0001537325,0.00003173171,0.00005639669,0.00007242916,0.001480295,0.9954293,0.002369593],"study_design_scores_gemma":[0.0001419445,0.00004473432,0.001687694,0.0003074112,0.00004586173,0.0001007454,0.0001242851,0.0001462692,0.00008066512,0.0006400155,0.9965927,0.00008757185],"study_design_candidate":"not_applicable","study_design_consensus":"not_applicable","genre_codex":"commentary","genre_gemma":"commentary","genre_scores_codex":[0.0004703573,0.002300202,0.0001825227,0.9279595,0.04188307,0.0003345456,0.00121823,0.0001321551,0.02551935],"genre_scores_gemma":[0.002105701,0.001234927,0.0004783126,0.9231477,0.009006945,0.0001795348,0.0004241084,0.00005573143,0.06336709],"genre_candidate":"commentary","genre_consensus":"commentary","teacher_disagreement_score":0.9487872,"threshold_uncertainty_score":0.7292688,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.03998037959415977,"score_gpt":0.362696304742736,"score_spread":0.3227159251485762,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}