{"id":"W2889177969","doi":"10.1007/978-1-4939-8651-4_32","title":"Morpholino-Mediated Exon Skipping Targeting Human ACVR1/ALK2 for Fibrodysplasia Ossificans Progressiva","year":2018,"lang":"en","type":"article","venue":"Methods in molecular biology","topic":"Heterotopic Ossification and Related Conditions","field":"Medicine","cited_by":6,"is_retracted":false,"has_abstract":false,"ca_institutions":"Muscular Dystrophy Canada; University of Alberta","funders":"Canadian Institutes of Health Research","keywords":"Fibrodysplasia ossificans progressiva; Morpholino; Myositis ossificans; Heterotopic ossification; Exon; Medicine; Ossification; Bioinformatics; Cancer research; Gene knockdown; Biology; Pathology; Genetics; Gene; Surgery","routes":{"ca_aff":true,"ca_fund":true,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"codex-gemma-dda1882f352a","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0008625152,0.0001858168,0.0003671458,0.0002638496,0.0001767943,0.00001600694,0.0001504556,0.0004066798,0.0002224748],"category_scores_gemma":[0.0009985031,0.0001590214,0.0001301482,0.000324865,0.000365566,0.00002399776,0.00004453334,0.0003271765,0.00002484493],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.00006058697,"about_ca_system_score_gemma":0.00007875315,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.00001371483,"about_ca_topic_score_gemma":0.000002500919,"domain_scores_codex":[0.9979829,0.0005182024,0.0005156414,0.0004730989,0.00007432738,0.0004357862],"domain_scores_gemma":[0.9990001,0.0001973809,0.0001533344,0.000364776,0.0001570289,0.000127347],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"bench_or_experimental","study_design_gemma":"bench_or_experimental","study_design_scores_codex":[0.00003335905,0.00009654513,0.002621923,0.0000429209,0.00006479035,0.00002277162,0.0002348086,0.000001136202,0.9859589,0.0025069,0.0001499256,0.008265957],"study_design_scores_gemma":[0.005041824,0.001540772,0.008819158,0.0003032807,0.000177353,0.0001169726,0.0003602788,0.003509542,0.8676241,0.007535444,0.10432,0.0006512808],"study_design_candidate":"bench_or_experimental","study_design_consensus":"bench_or_experimental","genre_codex":"methods","genre_gemma":"methods","genre_scores_codex":[0.1674514,0.0002791742,0.8261546,0.001584537,0.0004457993,0.001373362,0.00002072434,0.0001394364,0.002550909],"genre_scores_gemma":[0.2058875,0.00001219626,0.7917662,0.0008071196,0.0002741628,0.0004068672,0.0003911049,0.00003911408,0.000415754],"genre_candidate":"methods","genre_consensus":"methods","teacher_disagreement_score":0.1183349,"threshold_uncertainty_score":0.6484705,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.0440539712513361,"score_gpt":0.4611845499549108,"score_spread":0.4171305787035747,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}