{"id":"W2899663130","doi":"10.1182/blood-2018-99-111306","title":"Efficacy of Eculizumab in Pediatric Patients with Paroxysmal Nocturnal Hemoglobinuria in the International PNH Registry","year":2018,"lang":"en","type":"article","venue":"Blood","topic":"Complement system in diseases","field":"Immunology and Microbiology","cited_by":3,"is_retracted":false,"has_abstract":true,"ca_institutions":"University of Toronto; University Health Network","funders":"","keywords":"Eculizumab; Paroxysmal nocturnal hemoglobinuria; Medicine; Disease registry; Pediatrics; Cohort; Demographics; Hemoglobinuria; Internal medicine; Disease; Anemia; Immunology; Demography","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"codex-gemma-dda1882f352a","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0001403768,0.0000939234,0.0001314956,0.00009792185,0.00003104657,0.000008567327,0.0004264394,0.00005629767,0.0002943473],"category_scores_gemma":[0.00008452185,0.00006301993,0.00003397511,0.0001540093,0.00009374085,0.00003979592,0.00006597656,0.0001137735,0.0000502531],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0000205231,"about_ca_system_score_gemma":0.00006059791,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.00005653659,"about_ca_topic_score_gemma":0.0001539732,"domain_scores_codex":[0.999199,0.0001178536,0.0002765304,0.0001655647,0.00007357338,0.0001674718],"domain_scores_gemma":[0.9994479,0.0001036946,0.0001479283,0.0002318382,0.00006025088,0.000008399095],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"observational","study_design_gemma":"observational","study_design_scores_codex":[0.0003675988,0.001248982,0.9962189,0.0000157162,0.0000461406,0.000006013992,0.0003730006,0.000001447745,0.0003378655,0.00008289635,0.001188364,0.00011307],"study_design_scores_gemma":[0.009632537,0.0002260032,0.9878535,0.00003510914,0.0000434591,0.00001262554,0.0001012273,4.748757e-7,0.001136516,0.0000270176,0.000853414,0.0000781483],"study_design_candidate":"observational","study_design_consensus":"observational","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9977314,0.0002376543,0.000002140379,0.00007181033,0.0002558638,0.0002505716,0.00003729018,0.000008614843,0.00140462],"genre_scores_gemma":[0.9997018,0.000003411038,0.00002603066,0.00004111753,0.00008852167,0.00001623537,0.00007136519,0.000005613699,0.00004592813],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.009264939,"threshold_uncertainty_score":0.3222897,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.007753470290376171,"score_gpt":0.2268289054195395,"score_spread":0.2190754351291633,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}