{"id":"W2906423725","doi":"10.1016/j.jval.2018.09.150","title":"PCN68 - BUDGET IMPACT ANALYSIS OF TISAGENLECLEUCEL FOR THE TREATMENT OF PAEDIATRIC AND YOUNG ADULT PATIENTS WITH RELAPSED OR REFRACTORY B-CELL ACUTE LYMPHOBLASTIC LEUKAEMIA IN ENGLAND","year":2018,"lang":"en","type":"article","venue":"Value in Health","topic":"CAR-T cell therapy research","field":"Medicine","cited_by":4,"is_retracted":false,"has_abstract":false,"ca_institutions":"Novartis (Canada)","funders":"","keywords":"Blinatumomab; Medicine; Fludarabine; Population; Leukapheresis; Pediatrics; Internal medicine; Chemotherapy; CD19; Cyclophosphamide; Stem cell","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"codex-gemma-dda1882f352a","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0005146708,0.0001685857,0.00065395,0.0006450154,0.00004755147,0.000006294968,0.00008238994,0.00008207571,0.00007725227],"category_scores_gemma":[0.0001215607,0.00009112968,0.0001081635,0.001324281,0.0001235397,0.00003832427,0.00001469594,0.00009746036,7.747315e-7],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0007663934,"about_ca_system_score_gemma":0.0006826245,"about_ca_topic_candidate":true,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.01314501,"about_ca_topic_score_gemma":0.002900615,"domain_scores_codex":[0.9982703,0.0001896969,0.0005337743,0.00027996,0.0003599597,0.0003662772],"domain_scores_gemma":[0.9980555,0.0009489974,0.0002559366,0.0003878189,0.0002074398,0.0001442982],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"observational","study_design_gemma":"observational","study_design_scores_codex":[0.01242269,0.001510182,0.9593661,0.0003196109,0.0008284427,0.000009124947,0.007013498,0.0003020337,0.0008084503,0.000002462934,0.00004644056,0.01737099],"study_design_scores_gemma":[0.02583096,0.02759513,0.9217421,0.0001312258,0.0008183977,0.000004177488,0.0001874954,0.02252886,0.0007840437,0.00001016936,0.0002418059,0.0001256001],"study_design_candidate":"observational","study_design_consensus":"observational","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9973244,0.0008525275,0.00003815589,0.0000753952,0.00005474322,0.00147031,0.0001403775,0.000006535869,0.00003757256],"genre_scores_gemma":[0.9956931,0.003509902,0.0002766277,0.00003861629,0.0000637291,0.00005566492,0.00005173463,0.00002676154,0.0002838493],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.03762393,"threshold_uncertainty_score":0.9934266,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.02278561923704356,"score_gpt":0.3226940231777702,"score_spread":0.2999084039407267,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}