{"id":"W2906423725","doi":"10.1016/j.jval.2018.09.150","title":"PCN68 - BUDGET IMPACT ANALYSIS OF TISAGENLECLEUCEL FOR THE TREATMENT OF PAEDIATRIC AND YOUNG ADULT PATIENTS WITH RELAPSED OR REFRACTORY B-CELL ACUTE LYMPHOBLASTIC LEUKAEMIA IN ENGLAND","year":2018,"lang":"en","type":"article","venue":"Value in Health","topic":"CAR-T cell therapy research","field":"Medicine","cited_by":4,"is_retracted":false,"has_abstract":false,"ca_institutions":"Novartis (Canada)","funders":"","keywords":"Blinatumomab; Medicine; Fludarabine; Population; Leukapheresis; Pediatrics; Internal medicine; Chemotherapy; CD19; Cyclophosphamide; Stem cell","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.004850123,0.0006402315,0.001475333,0.001253371,0.0002771832,0.001630588,0.001106475,0.001081206,0.005711562],"category_scores_gemma":[0.01826742,0.000584729,0.002453714,0.001980674,0.0005464056,0.0009201326,0.00170081,0.001639918,0.0002864024],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.01866228,"about_ca_system_score_gemma":0.01571979,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.2256107,"about_ca_topic_score_gemma":0.2121392,"domain_scores_codex":[0.9926841,0.004387504,0.0003515982,0.0002148692,0.0008925298,0.001469492],"domain_scores_gemma":[0.9931804,0.00290177,0.001376614,0.0001560447,0.0008082391,0.001576978],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"simulation_or_modeling","study_design_gemma":"observational","study_design_scores_codex":[0.0658298,0.002080894,0.1134834,0.007096206,0.008660458,0.001693262,0.0005724521,0.51908,0.002073997,0.01659292,0.04309151,0.2197451],"study_design_scores_gemma":[0.02684185,0.02861974,0.631864,0.005256135,0.01024394,0.00182727,0.003918617,0.1691219,0.002550081,0.009112873,0.1102265,0.0004171151],"study_design_candidate":"observational","study_design_consensus":null,"genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9029527,0.01732462,0.00214311,0.01401486,0.0003637524,0.001854057,0.03644783,0.0001172616,0.02478196],"genre_scores_gemma":[0.9867736,0.002755407,0.000973389,0.001020489,0.00004799606,0.0004770084,0.005257983,0.00002412655,0.002670037],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.2256107,"threshold_uncertainty_score":0.4485949,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.02278561923704356,"score_gpt":0.3226940231777702,"score_spread":0.2999084039407267,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}