{"id":"W2913853823","doi":"10.1182/bloodadvances.2018023176","title":"Successful in utero stem cell transplantation in X-linked severe combined immunodeficiency","year":2019,"lang":"en","type":"article","venue":"Blood Advances","topic":"Immunodeficiency and Autoimmune Disorders","field":"Immunology and Microbiology","cited_by":15,"is_retracted":false,"has_abstract":true,"ca_institutions":"Université de Montréal; Centre Hospitalier Universitaire Sainte-Justine","funders":"","keywords":"In utero; Transplantation; Immunodeficiency; Sibling; Stem cell; Severe combined immunodeficiency; Medicine; Immunology; Immune system; Hematopoietic stem cell transplantation; Fetus; Pregnancy; Biology; Internal medicine; Psychology; Developmental psychology; Genetics","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"codex-gemma-dda1882f352a","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0002447514,0.0002353633,0.0003714846,0.0002337287,0.00008645857,0.00001800978,0.0003935613,0.0001909494,0.0002413339],"category_scores_gemma":[0.000004916948,0.0002248413,0.00007745775,0.0004142972,0.00009527708,0.0004604756,0.00003396661,0.0003703058,0.0004020247],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.00002363345,"about_ca_system_score_gemma":0.00005359955,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.000189806,"about_ca_topic_score_gemma":0.0000554809,"domain_scores_codex":[0.9983521,0.0001690053,0.0005173614,0.0004058087,0.00005042277,0.0005053045],"domain_scores_gemma":[0.9994045,0.0001221551,0.0001449473,0.0002975966,0.00002627844,0.000004540826],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"bench_or_experimental","study_design_gemma":"observational","study_design_scores_codex":[0.001398984,0.003241927,0.2735502,0.0006743582,0.00006309854,0.0000812031,0.009439665,0.003675711,0.6533248,0.001628262,0.000007239993,0.05291457],"study_design_scores_gemma":[0.05835642,0.00195568,0.6165251,0.001106275,0.0001593085,0.0003023428,0.02584279,0.0001419558,0.2706156,0.001320517,0.0209186,0.002755418],"study_design_candidate":"bench_or_experimental","study_design_consensus":null,"genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9368059,0.05624959,0.00001812422,0.00004768134,0.0007134993,0.0004264145,0.00001795113,0.00005718431,0.005663664],"genre_scores_gemma":[0.9964396,0.001779463,0.00001477743,0.00007117226,0.000001202414,0.00003505557,0.0001076417,0.00001684804,0.00153418],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.3827092,"threshold_uncertainty_score":0.9168762,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.004223471529893692,"score_gpt":0.2048873355451139,"score_spread":0.2006638640152202,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}