{"id":"W2913853823","doi":"10.1182/bloodadvances.2018023176","title":"Successful in utero stem cell transplantation in X-linked severe combined immunodeficiency","year":2019,"lang":"en","type":"article","venue":"Blood Advances","topic":"Immunodeficiency and Autoimmune Disorders","field":"Immunology and Microbiology","cited_by":15,"is_retracted":false,"has_abstract":true,"ca_institutions":"Université de Montréal; Centre Hospitalier Universitaire Sainte-Justine","funders":"","keywords":"In utero; Transplantation; Immunodeficiency; Sibling; Stem cell; Severe combined immunodeficiency; Medicine; Immunology; Immune system; Hematopoietic stem cell transplantation; Fetus; Pregnancy; Biology; Internal medicine; Psychology; Developmental psychology; Genetics","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0002878955,0.0002729232,0.0001958948,0.0003578368,0.0002360462,0.0002514343,0.0001975252,0.000561824,0.002577685],"category_scores_gemma":[0.0004573857,0.00004959554,0.000207441,0.0001484807,0.0002859923,0.0001267478,0.0002165362,0.0005163215,0.0005221213],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0001998263,"about_ca_system_score_gemma":0.0002312395,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.0002887876,"about_ca_topic_score_gemma":0.0004965206,"domain_scores_codex":[0.999926,0.0000144952,0.000008568195,0.00001205917,0.00002330243,0.00001563844],"domain_scores_gemma":[0.9998733,0.00004663684,0.00001731047,0.00002081331,0.000009392943,0.00003250493],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"design_other","study_design_gemma":"observational","study_design_scores_codex":[0.001281235,0.0009369798,0.05923157,0.0004245772,0.000181064,0.2205226,0.0004102373,0.00486475,0.1696279,0.01061094,0.01249273,0.5194155],"study_design_scores_gemma":[0.0003546048,0.003109534,0.1046629,0.0003569129,0.0003272697,0.6156517,0.0003223686,0.01086898,0.1458281,0.01000685,0.1084657,0.00004514047],"study_design_candidate":"observational","study_design_consensus":null,"genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9073015,0.01705067,0.03282567,0.002588456,0.00141456,0.0002035345,0.001077122,0.0005785968,0.03695976],"genre_scores_gemma":[0.9862837,0.003668617,0.004522462,0.0003255433,0.0002155304,0.00003542655,0.0004173579,0.00004099648,0.004490372],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.002577685,"threshold_uncertainty_score":0.008623242,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.004223471529893692,"score_gpt":0.2048873355451139,"score_spread":0.2006638640152202,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}