{"id":"W2937027974","doi":"","title":"RNA-based gene therapies for myotonic dystrophy type 1","year":2003,"lang":"en","type":"article","venue":"Corpus Université Laval (Université Laval)","topic":"Genetic Neurodegenerative Diseases","field":"Neuroscience","cited_by":3,"is_retracted":false,"has_abstract":true,"ca_institutions":"","funders":"","keywords":"Myotonic dystrophy; Gene; Medicine; Genetics; RNA; Bioinformatics; Biology; Computational biology; Neuroscience","routes":{"ca_aff":false,"ca_fund":false,"ca_venue":false,"about_ca":true,"invisible_to_affiliation_only":true},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"codex-gemma-dda1882f352a","candidate_categories":["metaepi_narrow"],"consensus_categories":[],"category_scores_codex":[0.0001067579,0.0004415012,0.0003692124,0.0003658369,0.0008135273,0.00007381554,0.000766751,0.0001383763,0.0001309868],"category_scores_gemma":[0.0002184423,0.0004892461,0.0003173225,0.0009148756,0.0002315897,0.0002475707,0.0001168295,0.0002001383,0.00005465737],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0003424139,"about_ca_system_score_gemma":0.0005460728,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.0001314444,"about_ca_topic_score_gemma":0.0001370803,"domain_scores_codex":[0.9973949,0.0003292312,0.0001940785,0.0009597222,0.0004534452,0.0006686492],"domain_scores_gemma":[0.998171,0.0003335751,0.0001999526,0.0006616415,0.0002915211,0.0003423559],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"bench_or_experimental","study_design_gemma":"bench_or_experimental","study_design_scores_codex":[0.0004535547,0.0001869321,0.001180864,0.00003108609,0.00003600324,0.0001778667,0.0007494951,0.0009295912,0.9752395,0.0190298,0.0005415422,0.001443761],"study_design_scores_gemma":[0.002441672,0.000570935,0.0009918771,0.00001370601,0.000158748,0.00001809038,0.0003916334,0.0003665257,0.9463252,0.0004042447,0.04780606,0.0005112955],"study_design_candidate":"bench_or_experimental","study_design_consensus":"bench_or_experimental","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9884531,0.0006095691,0.002067226,0.00067213,0.0006813983,0.0008218341,0.0001795519,0.0002667603,0.00624842],"genre_scores_gemma":[0.9896181,0.0004060077,0.001533821,0.000642252,0.00005497322,0.000005579664,0.00002503831,0.00007672528,0.007637483],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.04726452,"threshold_uncertainty_score":0.9997559,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.01835277878072575,"score_gpt":0.2085253642188171,"score_spread":0.1901725854380913,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}