{"id":"W2937027974","doi":"","title":"RNA-based gene therapies for myotonic dystrophy type 1","year":2003,"lang":"en","type":"article","venue":"Corpus Université Laval (Université Laval)","topic":"Genetic Neurodegenerative Diseases","field":"Neuroscience","cited_by":3,"is_retracted":false,"has_abstract":true,"ca_institutions":"","funders":"","keywords":"Myotonic dystrophy; Gene; Medicine; Genetics; RNA; Bioinformatics; Biology; Computational biology; Neuroscience","routes":{"ca_aff":false,"ca_fund":false,"ca_venue":false,"about_ca":true,"invisible_to_affiliation_only":true},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0003080128,0.000375756,0.0004361547,0.0003792929,0.0002627787,0.0004507951,0.0004113612,0.0006232155,0.003900453],"category_scores_gemma":[0.0002077674,0.0001338774,0.000481023,0.0001825672,0.0002871781,0.0002448325,0.0002851466,0.001014483,0.0007831096],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0005601285,"about_ca_system_score_gemma":0.0003086069,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.0009100504,"about_ca_topic_score_gemma":0.002421695,"domain_scores_codex":[0.9997959,0.00003784615,0.00001217446,0.00003921915,0.00007947876,0.0000354498],"domain_scores_gemma":[0.999949,0.00001661177,0.00001220466,0.000004613704,0.00001104318,0.000006605027],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"bench_or_experimental","study_design_gemma":"not_applicable","study_design_scores_codex":[0.000973323,0.0006601007,0.0004592981,0.001186117,0.000142792,0.0004863949,0.0001528587,0.001239614,0.8524569,0.007272881,0.004272044,0.1306977],"study_design_scores_gemma":[0.001664522,0.01222166,0.00725489,0.0007055419,0.000658053,0.003188923,0.0002822112,0.006714509,0.6735694,0.004598082,0.289045,0.00009712412],"study_design_candidate":"not_applicable","study_design_consensus":null,"genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.5801749,0.2621195,0.06849781,0.006111319,0.004193976,0.001347277,0.002691998,0.001442119,0.07342111],"genre_scores_gemma":[0.8148868,0.1015142,0.03151929,0.002171667,0.0004393236,0.00108604,0.002416125,0.0001496092,0.04581699],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.003900453,"threshold_uncertainty_score":0.01304829,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.01835277878072575,"score_gpt":0.2085253642188171,"score_spread":0.1901725854380913,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}