{"id":"W2985220055","doi":"","title":"Antisense oligonucleotides for the treatment of cardiomyopathy in Duchenne muscular dystrophy.","year":2019,"lang":"en","type":"article","venue":"PubMed","topic":"Muscle Physiology and Disorders","field":"Biochemistry, Genetics and Molecular Biology","cited_by":42,"is_retracted":false,"has_abstract":true,"ca_institutions":"Muscular Dystrophy Canada; University of Alberta","funders":"","keywords":"Duchenne muscular dystrophy; Dystrophin; Exon skipping; Cardiomyopathy; Medicine; Skeletal muscle; Muscular dystrophy; Myopathy; Bioinformatics; Myocyte; Internal medicine; Cardiology; Exon; Biology; Heart failure; Genetics; Alternative splicing; Gene","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"codex-gemma-dda1882f352a","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.00009306,0.00008791774,0.0001435212,0.00002263327,0.00002190882,0.000003650429,0.00008595655,0.00006250445,0.000003416927],"category_scores_gemma":[0.00002569619,0.00006078258,0.0001408696,0.00004536691,0.00005453037,0.000001667585,0.00001616194,0.00001766925,0.000001929435],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.00000821722,"about_ca_system_score_gemma":0.0000127307,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.00005298557,"about_ca_topic_score_gemma":0.00002186131,"domain_scores_codex":[0.9994293,0.00003049841,0.0001142017,0.0001886043,0.00003552053,0.0002018106],"domain_scores_gemma":[0.9995896,0.00002693633,0.00004060834,0.0002917447,0.00002557798,0.00002549355],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"bench_or_experimental","study_design_gemma":"observational","study_design_scores_codex":[0.002992005,0.00122025,0.1091273,0.0001946067,0.0009790014,0.000006983075,0.0003951875,0.004113085,0.5594568,0.0008354339,0.0007911283,0.3198882],"study_design_scores_gemma":[0.0030863,0.0005754764,0.8351275,0.000003304286,0.00005756982,0.000002529021,0.0001683127,0.0000829444,0.1183289,0.0001807239,0.04220185,0.000184557],"study_design_candidate":"observational","study_design_consensus":null,"genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9967161,0.001755659,0.00005123932,0.00008802646,0.0001554137,0.0009365719,0.00001738528,0.000003404513,0.0002761299],"genre_scores_gemma":[0.9983802,0.0005628499,0.00004128494,0.00004676983,0.00007164868,0.0007125849,0.00002518256,0.000009993868,0.0001494626],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.7260002,"threshold_uncertainty_score":0.2478642,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.009352826668584793,"score_gpt":0.2088087948189917,"score_spread":0.1994559681504069,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}