{"id":"W3002143230","doi":"10.3390/ijms21030733","title":"Genome Editing for the Understanding and Treatment of Inherited Cardiomyopathies","year":2020,"lang":"en","type":"review","venue":"International Journal of Molecular Sciences","topic":"CRISPR and Genetic Engineering","field":"Biochemistry, Genetics and Molecular Biology","cited_by":32,"is_retracted":false,"has_abstract":true,"ca_institutions":"Muscular Dystrophy Canada; University of Alberta","funders":"Faculty of Medicine and Dentistry, University of Alberta; Muscular Dystrophy Canada; University of Alberta; Canadian Institutes of Health Research; Women and Children's Health Research Institute; Children's Health Research Institute","keywords":"Transcription activator-like effector nuclease; Genome editing; Zinc finger nuclease; CRISPR; Duchenne muscular dystrophy; Cardiomyopathy; Biology; Genome; Computational biology; Genome engineering; Muscle disease; Genetics; Bioinformatics; Medicine; Disease; Gene; Heart failure; Internal medicine","routes":{"ca_aff":true,"ca_fund":true,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.000463188,0.0006844762,0.0008694557,0.001591265,0.0002239224,0.0006914585,0.0007126063,0.00115322,0.003299843],"category_scores_gemma":[0.0004814526,0.0001942661,0.000482998,0.0009812416,0.0004166875,0.0007672785,0.000593304,0.001987089,0.001391073],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0004331068,"about_ca_system_score_gemma":0.0006107256,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.000483365,"about_ca_topic_score_gemma":0.0007132466,"domain_scores_codex":[0.9998106,0.00003118124,0.00001868055,0.0000327451,0.0000861399,0.00002061396],"domain_scores_gemma":[0.9998029,0.0001138972,0.00002236579,0.000007353626,0.00003358963,0.0000198493],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"design_other","study_design_gemma":"not_applicable","study_design_scores_codex":[0.00005211316,0.00008053169,0.0001185596,0.01039127,0.00009436619,0.0003629088,0.00005393684,0.0004910151,0.007820074,0.008411854,0.02396531,0.9481581],"study_design_scores_gemma":[0.00002020247,0.0001001363,0.0004686191,0.001435804,0.00008816651,0.001948778,0.00002715866,0.0001503965,0.002050888,0.003000759,0.9906904,0.00001883376],"study_design_candidate":"not_applicable","study_design_consensus":null,"genre_codex":"review","genre_gemma":"review","genre_scores_codex":[0.000252135,0.9963034,0.0007216158,0.0003406503,0.0002861223,0.000008804524,0.000022096,0.0000242032,0.002040999],"genre_scores_gemma":[0.001563292,0.9964383,0.0006171717,0.0002461243,0.0001478392,0.00001028665,0.0000421838,0.000004241694,0.0009305055],"genre_candidate":"review","genre_consensus":"review","teacher_disagreement_score":0.003299843,"threshold_uncertainty_score":0.01103902,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.06121968719885937,"score_gpt":0.374863738915066,"score_spread":0.3136440517162067,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}