{"id":"W3003611538","doi":"10.1016/j.ymgme.2019.11.069","title":"Long-term treatment with elosulfase alfa has an acceptable safety profile for patients with Morquio syndrome type A: Real-world results from the Morquio A Registry Study (MARS)","year":2020,"lang":"en","type":"article","venue":"Molecular Genetics and Metabolism","topic":"Lysosomal Storage Disorders Research","field":"Medicine","cited_by":0,"is_retracted":false,"has_abstract":false,"ca_institutions":"McGill University Health Centre","funders":"","keywords":"Medicine; Poisson regression; Demography; Hazard ratio; Confidence interval; Proportional hazards model; Survival analysis; Residence; Cancer registry; Disease; Mortality rate; Cancer; Pediatrics; Environmental health; Internal medicine; Population","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.002805332,0.0001830527,0.0004637068,0.0002812768,0.0002384808,0.0008621484,0.0002412056,0.0003611603,0.001381063],"category_scores_gemma":[0.006575378,0.00008763,0.0007665451,0.0006194345,0.0002459759,0.0005160875,0.0003728687,0.0003780486,0.0001673478],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0004294062,"about_ca_system_score_gemma":0.0004047235,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.001289454,"about_ca_topic_score_gemma":0.001508003,"domain_scores_codex":[0.9987482,0.0006834258,0.0001306405,0.0001334328,0.0002239646,0.00008042849],"domain_scores_gemma":[0.9936753,0.001946252,0.003171597,0.0005116238,0.0003793187,0.0003158851],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"observational","study_design_gemma":"observational","study_design_scores_codex":[0.01256766,0.0001629445,0.9517822,0.000121369,0.0008595929,0.000295775,0.0001406914,0.0002117358,0.0023218,0.0001282487,0.001129595,0.03027824],"study_design_scores_gemma":[0.0007392322,0.002396481,0.9931481,0.00004275185,0.0003920222,0.000635522,0.0002047915,0.0002809876,0.0004855916,0.0001141547,0.001543288,0.00001698881],"study_design_candidate":"observational","study_design_consensus":"observational","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9965312,0.001406571,0.000219408,0.0003700324,0.00001584616,0.00001604298,0.0007783491,0.00001001865,0.0006526649],"genre_scores_gemma":[0.9983054,0.00033669,0.0002051455,0.0001617899,0.00002751958,0.00001328295,0.0008262303,0.000004483191,0.0001195401],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.002805332,"threshold_uncertainty_score":0.01483619,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.03328898209094625,"score_gpt":0.2890724796512562,"score_spread":0.2557834975603099,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}