{"id":"W3012393243","doi":"10.3390/genes11030342","title":"CRISPR-Generated Animal Models of Duchenne Muscular Dystrophy","year":2020,"lang":"en","type":"review","venue":"Genes","topic":"CRISPR and Genetic Engineering","field":"Biochemistry, Genetics and Molecular Biology","cited_by":25,"is_retracted":false,"has_abstract":true,"ca_institutions":"Muscular Dystrophy Canada; University of Alberta","funders":"Faculty of Medicine and Dentistry, University of Alberta; Muscular Dystrophy Canada; Canadian Institutes of Health Research; Women and Children's Health Research Institute","keywords":"CRISPR; Duchenne muscular dystrophy; Dystrophin; Genome editing; Muscular dystrophy; Neuromuscular disease; Computational biology; Medicine; Animal model; Disease; Biology; Bioinformatics; Genetics; Gene; Pathology","routes":{"ca_aff":true,"ca_fund":true,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"codex-gemma-dda1882f352a","candidate_categories":["metaepi_narrow"],"consensus_categories":[],"category_scores_codex":[0.00007629886,0.0004135338,0.0009565966,0.00006824166,0.00003192841,0.00001696456,0.0003365347,0.0003735275,0.00001667075],"category_scores_gemma":[0.00002344172,0.0003748842,0.0005332032,0.0001863689,0.00004271027,0.000002003473,0.0001873351,0.0001341528,0.00001231373],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.00001167439,"about_ca_system_score_gemma":0.0001642832,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.0000109468,"about_ca_topic_score_gemma":0.000002398459,"domain_scores_codex":[0.9985182,0.0000621331,0.0004773542,0.0005299401,0.0001414648,0.0002708801],"domain_scores_gemma":[0.9991355,0.000006594028,0.0001536851,0.0004904264,0.00009293157,0.0001208438],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"design_other","study_design_gemma":"not_applicable","study_design_scores_codex":[0.00002874549,0.00006134789,0.000001521695,0.01032374,0.0008937179,0.00003398697,0.00003069,0.002359023,0.09343999,0.00009824337,0.00150163,0.8912274],"study_design_scores_gemma":[0.0001325901,0.0001802866,7.013048e-7,0.0003535476,0.0003947128,0.00003021189,0.000007103445,0.0002436193,0.02006807,0.000006900472,0.978202,0.0003802494],"study_design_candidate":"not_applicable","study_design_consensus":null,"genre_codex":"review","genre_gemma":"review","genre_scores_codex":[0.0004374889,0.9910703,0.007733896,0.000009218129,0.0001877723,0.000299205,0.0001324032,0.00002043854,0.0001092482],"genre_scores_gemma":[0.001509621,0.9954159,0.001726565,0.00001384111,0.0006189958,0.0000493815,0.0004776499,0.00008919232,0.00009881243],"genre_candidate":"review","genre_consensus":"review","teacher_disagreement_score":0.9767004,"threshold_uncertainty_score":0.9998703,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.02712388646830918,"score_gpt":0.3267586569727555,"score_spread":0.2996347705044463,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}