{"id":"W3030936584","doi":"10.1111/hae.14015","title":"World Federation of Hemophilia Gene Therapy Registry","year":2020,"lang":"en","type":"article","venue":"Haemophilia","topic":"Hemophilia Treatment and Research","field":"Medicine","cited_by":51,"is_retracted":false,"has_abstract":true,"ca_institutions":"McMaster University; Canadian Hemophilia Society","funders":"National Heart, Lung, and Blood Institute","keywords":"Medicine; Haemophilia; Clinical trial; Genetic enhancement; Haemophilia A; Intensive care medicine; Pediatrics; Internal medicine; Gene","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.002497756,0.0005070181,0.0008173286,0.003248726,0.0006702751,0.002662197,0.001298993,0.001142496,0.1244173],"category_scores_gemma":[0.00653929,0.0002588414,0.0005524379,0.004851564,0.0003047455,0.001313256,0.001001336,0.001380883,0.07675963],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.001324973,"about_ca_system_score_gemma":0.004580043,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.00419687,"about_ca_topic_score_gemma":0.0025872,"domain_scores_codex":[0.9980145,0.000328177,0.0003430702,0.0003027795,0.0007801423,0.0002313554],"domain_scores_gemma":[0.9944371,0.0006366044,0.001334745,0.0007786143,0.001850175,0.0009628349],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"not_applicable","study_design_gemma":"observational","study_design_scores_codex":[0.0002154663,0.00004542583,0.003231079,0.0003279369,0.00002417873,0.0001181741,0.00002637405,0.00008981679,0.0002041852,0.003881775,0.9301587,0.06167698],"study_design_scores_gemma":[0.00009141434,0.00003412421,0.005860972,0.0004803884,0.00002258606,0.0004488559,0.000031211,0.0001134111,0.0002635679,0.0007349301,0.9919037,0.0000148192],"study_design_candidate":"observational","study_design_consensus":null,"genre_codex":"dataset","genre_gemma":"empirical","genre_scores_codex":[0.009712026,0.0279151,0.005280438,0.01684422,0.00590839,0.001339788,0.5295098,0.003079858,0.4004103],"genre_scores_gemma":[0.05061638,0.03433303,0.006649657,0.01032056,0.002273517,0.002505768,0.7177308,0.001355258,0.1742151],"genre_candidate":"empirical","genre_consensus":null,"teacher_disagreement_score":0.1244173,"threshold_uncertainty_score":0.4162173,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.0755540419877082,"score_gpt":0.3207616212898888,"score_spread":0.2452075793021806,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}