{"id":"W3037972267","doi":"10.1002/psb.1848","title":"Making sense of antisense oligonucleotide therapy","year":2020,"lang":"en","type":"article","venue":"Prescriber","topic":"Neurogenetic and Muscular Disorders Research","field":"Medicine","cited_by":3,"is_retracted":false,"has_abstract":true,"ca_institutions":"World Federation of Science Journalists","funders":"","keywords":"Spinal muscular atrophy; Medicine; Antisense therapy; Duchenne muscular dystrophy; Oligonucleotide; Neuromuscular disease; Muscular dystrophy; Disease; Sense (electronics); Bioinformatics; Neuroscience; Internal medicine; Genetics; Gene; Biology","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.003267359,0.0005890544,0.0006457093,0.0006573889,0.000676851,0.002844827,0.0008463245,0.002776273,0.008473473],"category_scores_gemma":[0.004881244,0.000335014,0.000590776,0.0002671232,0.00232694,0.002641213,0.002115859,0.006450504,0.003287206],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0007401811,"about_ca_system_score_gemma":0.0009353746,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.000434609,"about_ca_topic_score_gemma":0.0007732906,"domain_scores_codex":[0.9979116,0.0005964439,0.000130307,0.0003105363,0.0008609449,0.00019021],"domain_scores_gemma":[0.9982393,0.0008538855,0.000165156,0.0001550658,0.0003797532,0.0002069159],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"design_other","study_design_gemma":"not_applicable","study_design_scores_codex":[0.000472293,0.0002838022,0.001452829,0.001674514,0.0001605573,0.001506945,0.001498928,0.001331901,0.08937076,0.2724372,0.1195323,0.510278],"study_design_scores_gemma":[0.0001019924,0.0004469847,0.000305543,0.0003795772,0.00006400444,0.00112784,0.0003126001,0.0004009687,0.02473336,0.05302264,0.9190573,0.00004714039],"study_design_candidate":"not_applicable","study_design_consensus":null,"genre_codex":"commentary","genre_gemma":"review","genre_scores_codex":[0.03114936,0.2364791,0.1702405,0.2577119,0.07489306,0.0006432962,0.00083914,0.002169146,0.2258745],"genre_scores_gemma":[0.324541,0.2652372,0.07323898,0.1589843,0.02172955,0.0009479571,0.0009554868,0.0006450309,0.1537204],"genre_candidate":"review","genre_consensus":null,"teacher_disagreement_score":0.008473473,"threshold_uncertainty_score":0.02834666,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.1698099961990399,"score_gpt":0.3588922902539375,"score_spread":0.1890822940548976,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}