{"id":"W3047515600","doi":"10.1016/j.atherosclerosis.2020.07.028","title":"Lomitapide for treatment of homozygous familial hypercholesterolemia: The Québec experience","year":2020,"lang":"en","type":"article","venue":"Atherosclerosis","topic":"Lipoproteins and Cardiovascular Health","field":"Medicine","cited_by":21,"is_retracted":false,"has_abstract":false,"ca_institutions":"Montreal Clinical Research Institute; Université du Québec à Chicoutimi; McGill University; Université de Montréal; Université Laval; McGill University Health Centre","funders":"Dow AgroSciences; Instituto Danone; Dairy Australia; Medicines Company; Flax Council of Canada; Canola Council of Canada; Amarin Corporation; Ionis Pharmaceuticals; Dairy Farmers of Canada; Regeneron Pharmaceuticals; Novartis; Chiesi Farmaceutici; AstraZeneca; Amgen; Pfizer; Fondation Leducq; Danone Institute North America; Sanofi; Merck","keywords":"Familial hypercholesterolemia; Medicine; Internal medicine; Cholesterol","routes":{"ca_aff":true,"ca_fund":true,"ca_venue":false,"about_ca":true,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"codex-gemma-dda1882f352a","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0001042551,0.0001477508,0.0004207402,0.00001314187,0.0001051136,0.00001048002,0.0001112751,0.00006953644,0.00002173118],"category_scores_gemma":[0.00006733514,0.0000877584,0.0004148125,0.0001120661,0.0001098431,0.00003534069,0.00002109882,0.00004603638,0.00001361361],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0001015792,"about_ca_system_score_gemma":0.0001660841,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.005373824,"about_ca_topic_score_gemma":0.0003038064,"domain_scores_codex":[0.9989895,0.00004022422,0.0002544231,0.000260907,0.0002342114,0.0002207832],"domain_scores_gemma":[0.9991885,0.00006857793,0.00006582661,0.0004632425,0.00006470358,0.0001490928],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"design_other","study_design_gemma":"observational","study_design_scores_codex":[0.001824435,0.001410841,0.07878634,0.0006578143,0.001245133,0.00001646326,0.07165574,0.00006471651,0.3167059,0.0003085517,0.002126497,0.5251976],"study_design_scores_gemma":[0.02515335,0.01675764,0.3617234,0.0003211963,0.001659039,0.0001016205,0.01113511,0.001007438,0.2590438,0.00004938664,0.3222037,0.000844447],"study_design_candidate":"bench_or_experimental","study_design_consensus":null,"genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9913298,0.001029914,0.0009873855,0.005286015,0.00006959535,0.001084246,0.00002592281,0.00004237156,0.0001447809],"genre_scores_gemma":[0.9961575,0.0005025403,0.0005873386,0.001892153,0.0003746874,0.0003509324,0.000004883123,0.00003019747,0.00009972266],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.5243532,"threshold_uncertainty_score":0.8123651,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.066552303807905,"score_gpt":0.2857416877740859,"score_spread":0.2191893839661809,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}