{"id":"W3097650039","doi":"10.1002/ppul.25079","title":"The effect of emerging molecular and genetic therapies on cardiopulmonary disease in Duchenne muscular dystrophy","year":2020,"lang":"en","type":"review","venue":"Pediatric Pulmonology","topic":"Muscle Physiology and Disorders","field":"Biochemistry, Genetics and Molecular Biology","cited_by":2,"is_retracted":false,"has_abstract":true,"ca_institutions":"Ottawa Hospital; University of Ottawa","funders":"","keywords":"Medicine; Duchenne muscular dystrophy; Muscular dystrophy; Clinical trial; Cardiomyopathy; Disease; Respiratory failure; Neuromuscular disease; Genetic enhancement; Cardiology; Intensive care medicine; Heart failure; Pediatrics; Internal medicine; Gene; Genetics","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0005056966,0.0006708486,0.001334861,0.001625317,0.0001962934,0.0007735324,0.0007057969,0.0009803178,0.003095625],"category_scores_gemma":[0.0006704477,0.0001851901,0.0005032689,0.001234422,0.0002764693,0.0008434408,0.0004952028,0.001438348,0.001474958],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.00035557,"about_ca_system_score_gemma":0.000609521,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.0004710756,"about_ca_topic_score_gemma":0.001111674,"domain_scores_codex":[0.9998662,0.00002776612,0.00002515086,0.00002404994,0.00004403291,0.00001284461],"domain_scores_gemma":[0.9996957,0.0001820835,0.00003656188,0.000007064872,0.00005474792,0.00002391256],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"design_other","study_design_gemma":"not_applicable","study_design_scores_codex":[0.0001455498,0.00008365701,0.0001563682,0.0227032,0.0001252343,0.0002451953,0.00004750767,0.000323462,0.001936087,0.002017909,0.01793174,0.9542841],"study_design_scores_gemma":[0.00005229863,0.0003084173,0.001534693,0.008499024,0.0003315414,0.002273136,0.00007588461,0.0001174579,0.0007661744,0.002030275,0.9839813,0.00002974318],"study_design_candidate":"not_applicable","study_design_consensus":null,"genre_codex":"review","genre_gemma":"review","genre_scores_codex":[0.0001031469,0.9991301,0.00005837373,0.0001368761,0.0001218875,0.000002735448,0.00001348713,0.00000437889,0.0004290664],"genre_scores_gemma":[0.0004789659,0.9988594,0.0001061554,0.0001483747,0.0001274815,0.000005135,0.00002223298,0.000001031553,0.0002512425],"genre_candidate":"review","genre_consensus":"review","teacher_disagreement_score":0.003095625,"threshold_uncertainty_score":0.01035589,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.005194753963747636,"score_gpt":0.2499358457262665,"score_spread":0.2447410917625188,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}