{"id":"W3101964747","doi":"10.1016/j.jval.2020.10.006","title":"Independent Registries Are Cost-Effective Tools to Provide Mandatory Postauthorization Surveillance for Orphan Medicinal Products","year":2020,"lang":"en","type":"article","venue":"Value in Health","topic":"Health Systems, Economic Evaluations, Quality of Life","field":"Economics, Econometrics and Finance","cited_by":12,"is_retracted":false,"has_abstract":false,"ca_institutions":"University of British Columbia Hospital; Dalhousie University; University of Toronto; Nova Scotia Health Authority; University of Manitoba; Université de Montréal; University of British Columbia","funders":"","keywords":"Authorization; Medicine; Business; Data quality; Disease registry; Family medicine; Disease; Computer science; Marketing; Pathology","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.05814314,0.001017945,0.001283049,0.01252589,0.0006099691,0.003679853,0.001910616,0.00149333,0.01317687],"category_scores_gemma":[0.2131442,0.0009673053,0.001581923,0.01065011,0.0004925599,0.005310787,0.002881592,0.001832658,0.004993046],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.001436454,"about_ca_system_score_gemma":0.007518743,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.004419316,"about_ca_topic_score_gemma":0.005590203,"domain_scores_codex":[0.9531209,0.02825702,0.008458641,0.002211763,0.006947923,0.001003801],"domain_scores_gemma":[0.5878307,0.1900215,0.1227542,0.04748737,0.04560879,0.006297507],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"design_other","study_design_gemma":"observational","study_design_scores_codex":[0.00178946,0.0009805234,0.2617518,0.001372448,0.0009329124,0.0001801067,0.0003417188,0.003287565,0.000570889,0.01054697,0.1396047,0.5786411],"study_design_scores_gemma":[0.002913699,0.00278184,0.5665259,0.003931846,0.002489688,0.001300823,0.001016864,0.04026012,0.008987708,0.02768115,0.3416158,0.000494605],"study_design_candidate":"observational","study_design_consensus":null,"genre_codex":"methods","genre_gemma":"empirical","genre_scores_codex":[0.2598999,0.0140813,0.2903004,0.03193521,0.003460584,0.01593371,0.1850234,0.01139072,0.1879749],"genre_scores_gemma":[0.6530241,0.0088348,0.2086161,0.006496821,0.003036827,0.007835914,0.09627382,0.0008734623,0.01500822],"genre_candidate":"empirical","genre_consensus":null,"teacher_disagreement_score":0.05814314,"threshold_uncertainty_score":0.307494,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.4344236756413911,"score_gpt":0.4244410568005831,"score_spread":0.009982618840807977,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}