{"id":"W3112179900","doi":"10.1056/nejmoa2031054","title":"CRISPR-Cas9 Gene Editing for Sickle Cell Disease and β-Thalassemia","year":2020,"lang":"en","type":"article","venue":"New England Journal of Medicine","topic":"Hemoglobinopathies and Related Disorders","field":"Medicine","cited_by":1856,"is_retracted":false,"has_abstract":true,"ca_institutions":"SickKids Foundation; Hospital for Sick Children; University of Toronto; BC Children's Hospital; University of British Columbia","funders":"BC Children's Hospital; St. Jude Children's Research Hospital","keywords":"CRISPR; Thalassemia; Genome editing; Disease; Cas9; Medicine; Biology; Gene; Genetics; Internal medicine","routes":{"ca_aff":true,"ca_fund":true,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.01668992070907199,"score_gpt":0.2601342652765965,"score_spread":0.2434443445675245,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}