{"id":"W3133945301","doi":"10.3233/jnd-200611","title":"Improving Care and Empowering Adults Living with SMA: A Call to Action in the New Treatment Era","year":2021,"lang":"en","type":"letter","venue":"Journal of Neuromuscular Diseases","topic":"Neurogenetic and Muscular Disorders Research","field":"Medicine","cited_by":27,"is_retracted":false,"has_abstract":true,"ca_institutions":"McGill University","funders":"Muscular Dystrophy Canada; Cure SMA","keywords":"SMA*; Medicine; Spinal muscular atrophy; Quality of life (healthcare); Gerontology; Action (physics); Call to action; Nursing; Disease; Business; Pathology","routes":{"ca_aff":true,"ca_fund":true,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"codex-gemma-dda1882f352a","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.00007744409,0.000320279,0.0005632274,0.0003425243,0.00007707374,0.0001308097,0.00017343,0.0001330349,0.0000183398],"category_scores_gemma":[0.0002733984,0.0001947935,0.0003452148,0.0002686878,0.00003691943,0.00007605432,0.00006939198,0.001033085,0.000001113568],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0001408383,"about_ca_system_score_gemma":0.0008659458,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.0001841282,"about_ca_topic_score_gemma":0.0001079312,"domain_scores_codex":[0.9977504,0.0002683353,0.0003573068,0.0003891517,0.0008803391,0.0003544694],"domain_scores_gemma":[0.9987254,0.0001826181,0.0001894035,0.0004061784,0.0002102638,0.0002861647],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"design_other","study_design_gemma":"observational","study_design_scores_codex":[0.002597144,0.001786798,0.06161996,0.0100697,0.0021921,0.1626213,0.01681311,0.0003777185,0.006234037,9.460738e-7,0.1543805,0.5813068],"study_design_scores_gemma":[0.01123301,0.01828409,0.472578,0.01099044,0.004773254,0.01149445,0.009813676,0.00009012445,0.0003815204,0.000004500151,0.4592142,0.001142764],"study_design_candidate":"not_applicable","study_design_consensus":null,"genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.8812718,0.02277056,0.0001274238,0.09462684,0.0001708332,0.0009660287,0.00001252675,0.00001216811,0.00004184503],"genre_scores_gemma":[0.7946824,0.01058221,0.001025501,0.1870282,0.005698036,0.0001070921,0.00008857546,0.0003089844,0.0004789977],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.580164,"threshold_uncertainty_score":0.7943447,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.01783488637163309,"score_gpt":0.2906010424110547,"score_spread":0.2727661560394216,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}