{"id":"W3163890534","doi":"10.1002/mds.28642","title":"Rational Design of Novel Therapies for Pantothenate <scp>Kinase–Associated</scp> Neurodegeneration","year":2021,"lang":"en","type":"review","venue":"Movement Disorders","topic":"Neurological diseases and metabolism","field":"Neuroscience","cited_by":22,"is_retracted":false,"has_abstract":true,"ca_institutions":"PQ Corporation (Canada)","funders":"National Institute of Neurological Disorders and Stroke","keywords":"Clinical trial; Dystonia; Neurodegeneration; Medicine; Neuroscience; Bioinformatics; Psychology; Internal medicine; Biology; Disease","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0007239701,0.001041875,0.001294356,0.0007090086,0.000302366,0.00107425,0.0009876366,0.001056004,0.003442458],"category_scores_gemma":[0.0004025317,0.0004301021,0.001151577,0.0003176414,0.0004869191,0.0009520366,0.0006169939,0.001955015,0.001505402],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0008522401,"about_ca_system_score_gemma":0.0009514359,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.0004667829,"about_ca_topic_score_gemma":0.001358767,"domain_scores_codex":[0.9997496,0.00005974846,0.00002174189,0.00003988974,0.00006505995,0.0000640049],"domain_scores_gemma":[0.9998634,0.00003000806,0.00003610929,0.000008934328,0.00003378439,0.00002780858],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"bench_or_experimental","study_design_gemma":"not_applicable","study_design_scores_codex":[0.002219808,0.001614187,0.0009968412,0.0152093,0.0009326402,0.002816701,0.0003012598,0.02944569,0.5262452,0.03031174,0.01660826,0.3732983],"study_design_scores_gemma":[0.00459696,0.01713006,0.001956827,0.002122877,0.001325391,0.004164946,0.0002502067,0.01744219,0.1911098,0.01482469,0.7448039,0.0002722034],"study_design_candidate":"not_applicable","study_design_consensus":null,"genre_codex":"review","genre_gemma":"review","genre_scores_codex":[0.1826125,0.6318006,0.1243075,0.009882377,0.002878556,0.00397615,0.002186308,0.001058663,0.04129744],"genre_scores_gemma":[0.4347081,0.4560329,0.0887716,0.004658045,0.0007263678,0.002479947,0.002613011,0.000156551,0.009853592],"genre_candidate":"review","genre_consensus":"review","teacher_disagreement_score":0.003442458,"threshold_uncertainty_score":0.01151621,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.1152602105450928,"score_gpt":0.3240386251320939,"score_spread":0.2087784145870011,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}