{"id":"W3166852472","doi":"10.1016/j.nmd.2021.06.001","title":"Health related quality of life in young, steroid-naïve boys with Duchenne muscular dystrophy","year":2021,"lang":"en","type":"article","venue":"Neuromuscular Disorders","topic":"Muscle Physiology and Disorders","field":"Biochemistry, Genetics and Molecular Biology","cited_by":8,"is_retracted":false,"has_abstract":false,"ca_institutions":"Western University","funders":"Medical Research Council; National Institutes of Health; Università degli Studi di Messina; National Institute of Neurological Disorders and Stroke; Parent Project Muscular Dystrophy; Action Duchenne; Muscular Dystrophy Canada; Muscular Dystrophy Association; Sarepta Therapeutics; Children's National Hospital; Università degli Studi di Padova; Virginia Commonwealth University; Vanderbilt University; PTC Therapeutics","keywords":"Duchenne muscular dystrophy; Health related quality of life; Medicine; Quality of life (healthcare); Muscular dystrophy; Internal medicine; Disease","routes":{"ca_aff":true,"ca_fund":true,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"codex-gemma-dda1882f352a","candidate_categories":["metaepi_narrow"],"consensus_categories":[],"category_scores_codex":[0.0003263154,0.0002878659,0.0005577076,0.00008212677,0.00008550098,0.0000126166,0.000238924,0.0002091335,0.00004408017],"category_scores_gemma":[0.0002801734,0.0002814402,0.0002421261,0.0003879836,0.0002188305,0.00001137609,0.0001257851,0.0002618945,0.000005398847],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.00001513593,"about_ca_system_score_gemma":0.0003580327,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.001045784,"about_ca_topic_score_gemma":0.004889726,"domain_scores_codex":[0.9972098,0.00066991,0.0006573194,0.0007532327,0.0002521573,0.0004575981],"domain_scores_gemma":[0.9986092,0.00002275844,0.0002809812,0.0008222174,0.0001016655,0.0001632078],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"bench_or_experimental","study_design_gemma":"observational","study_design_scores_codex":[0.002684246,0.002956852,0.4818057,0.001120907,0.000986944,0.00005356138,0.001026318,0.009819781,0.4909283,0.001599152,0.000907621,0.00611058],"study_design_scores_gemma":[0.007188041,0.001420761,0.9818277,0.00006323161,0.00004127874,0.00001990128,0.001040474,0.0001032712,0.004386616,0.0007323059,0.002428973,0.0007474868],"study_design_candidate":"observational","study_design_consensus":null,"genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9943554,0.002926735,0.0003690817,0.001021908,0.0001384717,0.0003102883,0.00002149309,0.00002144022,0.0008351525],"genre_scores_gemma":[0.9979365,0.0008008217,0.0002225044,0.0005253822,0.00002300724,0.00003166805,0.0003138212,0.00004685851,0.00009946011],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.5000219,"threshold_uncertainty_score":0.9999638,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.009644000662307277,"score_gpt":0.2455037114724755,"score_spread":0.2358597108101683,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}