{"id":"W3166852472","doi":"10.1016/j.nmd.2021.06.001","title":"Health related quality of life in young, steroid-naïve boys with Duchenne muscular dystrophy","year":2021,"lang":"en","type":"article","venue":"Neuromuscular Disorders","topic":"Muscle Physiology and Disorders","field":"Biochemistry, Genetics and Molecular Biology","cited_by":8,"is_retracted":false,"has_abstract":false,"ca_institutions":"Western University","funders":"Medical Research Council; National Institutes of Health; Università degli Studi di Messina; National Institute of Neurological Disorders and Stroke; Parent Project Muscular Dystrophy; Action Duchenne; Muscular Dystrophy Canada; Muscular Dystrophy Association; Sarepta Therapeutics; Children's National Hospital; Università degli Studi di Padova; Virginia Commonwealth University; Vanderbilt University; PTC Therapeutics","keywords":"Duchenne muscular dystrophy; Health related quality of life; Medicine; Quality of life (healthcare); Muscular dystrophy; Internal medicine; Disease","routes":{"ca_aff":true,"ca_fund":true,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0002140567,0.0002467212,0.0004782541,0.0005610479,0.0004827876,0.0004696496,0.0001975606,0.0004468143,0.00135321],"category_scores_gemma":[0.00104243,0.000172161,0.0003226939,0.000384199,0.0002945233,0.0002870407,0.0003091788,0.0005252768,0.0002036358],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0003530212,"about_ca_system_score_gemma":0.0001904941,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.007968038,"about_ca_topic_score_gemma":0.007863032,"domain_scores_codex":[0.9998366,0.00004586962,0.00001489028,0.00002549316,0.00003346893,0.00004369145],"domain_scores_gemma":[0.999437,0.0001239113,0.0001411233,0.00001308692,0.00005385226,0.0002310085],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"observational","study_design_gemma":"observational","study_design_scores_codex":[0.0002201743,0.0001759551,0.9951958,0.00001736934,0.00003229876,0.0009774562,0.0004428591,0.00006329649,0.0004972755,0.00001413152,0.0001122099,0.002251099],"study_design_scores_gemma":[0.000007163627,0.0003203104,0.9984027,0.000003423922,0.00001231532,0.0007160315,0.0003794011,0.00005329029,0.00003245099,0.000005607988,0.00006486427,0.00000253266],"study_design_candidate":"observational","study_design_consensus":"observational","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9994357,0.0001670646,0.00001253186,0.00003032261,0.000004441349,0.000003160834,0.0001034476,0.000001990695,0.0002413421],"genre_scores_gemma":[0.9995632,0.00007554788,0.00001627876,0.00001856501,0.00000396494,0.000003236916,0.0001070009,6.502946e-7,0.0002116563],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.007968038,"threshold_uncertainty_score":0.01584333,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.009644000662307277,"score_gpt":0.2455037114724755,"score_spread":0.2358597108101683,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}