{"id":"W3174394828","doi":"10.1017/cjn.2019.164","title":"P.064 FIREFISH Part 1: 1-year results on motor function in infants with Type 1 spinal muscular atrophy (SMA) receiving risdiplam (RG7916)","year":2019,"lang":"en","type":"article","venue":"Canadian Journal of Neurological Sciences / Journal Canadien des Sciences Neurologiques","topic":"Neurogenetic and Muscular Disorders Research","field":"Medicine","cited_by":6,"is_retracted":false,"has_abstract":true,"ca_institutions":"Canadian Celiac Association","funders":"","keywords":"SMN1; SMA*; Spinal muscular atrophy; Medicine; Tolerability; Interim analysis; Internal medicine; Oncology; Adverse effect; Clinical trial","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":true,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.002105089,0.0006464891,0.00112436,0.0003059434,0.0004073327,0.0005342331,0.000524172,0.0009953286,0.003047599],"category_scores_gemma":[0.001211955,0.0001568802,0.001328891,0.0002116455,0.0004624876,0.0005215321,0.0004779427,0.001268276,0.0006917772],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0007757132,"about_ca_system_score_gemma":0.0009457722,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.001722566,"about_ca_topic_score_gemma":0.001867987,"domain_scores_codex":[0.9994598,0.0001991784,0.00003825082,0.00007081163,0.0001073965,0.0001246358],"domain_scores_gemma":[0.9989607,0.0001752122,0.0001905529,0.0001240505,0.0001278355,0.0004217248],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"randomized_trial","study_design_gemma":"randomized_trial","study_design_scores_codex":[0.6113934,0.05047816,0.07323269,0.00066613,0.001733514,0.001933447,0.0004532693,0.00173478,0.04881824,0.0002546448,0.01758408,0.1917177],"study_design_scores_gemma":[0.03634848,0.7016083,0.2396188,0.0001212449,0.0008216152,0.001375553,0.0001325798,0.0008791619,0.01078636,0.0001273323,0.008119528,0.00006110164],"study_design_candidate":"randomized_trial","study_design_consensus":"randomized_trial","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9891818,0.001747923,0.0004990245,0.0005111254,0.00008659218,0.0007048094,0.004796553,0.00008842562,0.002383869],"genre_scores_gemma":[0.9804361,0.0009924571,0.001556834,0.0008893979,0.0001072993,0.0007098794,0.0117784,0.00003309878,0.003496646],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.003047599,"threshold_uncertainty_score":0.0111329,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.0309815833772258,"score_gpt":0.2780816557645343,"score_spread":0.2471000723873085,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}