{"id":"W3184889104","doi":"10.1007/s12325-021-01825-4","title":"Real-World Healthcare Resource Utilization (HRU) and Costs of Patients with Paroxysmal Nocturnal Hemoglobinuria (PNH) Receiving Eculizumab in a US Population","year":2021,"lang":"en","type":"article","venue":"Advances in Therapy","topic":"Complement system in diseases","field":"Immunology and Microbiology","cited_by":32,"is_retracted":false,"has_abstract":true,"ca_institutions":"Group for Research in Decision Analysis","funders":"Apellis Pharmaceuticals","keywords":"Eculizumab; Medicine; Paroxysmal nocturnal hemoglobinuria; Discontinuation; Cohort; Population; Internal medicine; Pediatrics; Retrospective cohort study; Immunology","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"codex-gemma-dda1882f352a","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0001240972,0.0001271084,0.0002555409,0.0001290915,0.00005580034,0.000007793245,0.00007924499,0.00005801096,0.00008465293],"category_scores_gemma":[0.00003418228,0.0001136145,0.00002105428,0.0003269335,0.00007131568,0.0001755248,0.00002939346,0.0001074925,9.718535e-7],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0001454103,"about_ca_system_score_gemma":0.00004129153,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.0008559714,"about_ca_topic_score_gemma":0.0129417,"domain_scores_codex":[0.998702,0.0003951187,0.0003773761,0.0002656104,0.00006133259,0.0001985389],"domain_scores_gemma":[0.9993956,0.0001179248,0.000207389,0.0001854234,0.0000773435,0.00001633586],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"observational","study_design_gemma":"observational","study_design_scores_codex":[0.0008639577,0.0001234076,0.9576825,0.00004684486,0.00001608302,0.000002896311,0.0003164163,0.0001515654,0.0003602805,0.0004056455,0.00001284097,0.04001758],"study_design_scores_gemma":[0.003421258,0.0001672383,0.9913095,0.0003915405,0.000004289964,0.000003811537,0.0002829883,0.00001113809,0.001353634,0.0002399641,0.002691229,0.0001234662],"study_design_candidate":"observational","study_design_consensus":"observational","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9838396,0.01532395,0.00001675862,0.00009132347,0.0001399014,0.0003544726,0.00003844245,0.00001647124,0.0001790767],"genre_scores_gemma":[0.9977189,0.001607703,0.0001224854,0.00006661644,0.00001027885,0.00002331123,0.0004030209,0.00001262855,0.00003510118],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.03989411,"threshold_uncertainty_score":0.722177,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.01518216342370635,"score_gpt":0.2951789799775904,"score_spread":0.279996816553884,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}