{"id":"W3203864936","doi":"10.1212/wnl.96.15_supplement.2240","title":"SUNFISH Part 2: 24-month Efficacy and Safety of Risdiplam in Patients with Type 2 or Non-ambulant Type 3 Spinal Muscular Atrophy (SMA) (2240)","year":2021,"lang":"en","type":"article","venue":"Neurology","topic":"Neurogenetic and Muscular Disorders Research","field":"Medicine","cited_by":2,"is_retracted":false,"has_abstract":true,"ca_institutions":"McGill University","funders":"","keywords":"SMA*; Spinal muscular atrophy; Medicine; Physical medicine and rehabilitation; Atrophy; Physical therapy; Pediatrics; Internal medicine; Disease","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"codex-gemma-dda1882f352a","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.00009276382,0.000148482,0.0003937713,0.0001010221,0.00003442942,0.000005660276,0.00007880227,0.0001140224,0.0001753237],"category_scores_gemma":[0.0001854351,0.000112064,0.0000402179,0.0003934417,0.0001566548,0.00001948031,0.0001002975,0.0003265758,0.00001180973],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.000008139441,"about_ca_system_score_gemma":0.0002307673,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.00004005129,"about_ca_topic_score_gemma":0.000111858,"domain_scores_codex":[0.9985873,0.0001402853,0.0002458197,0.0004101096,0.000289328,0.0003272089],"domain_scores_gemma":[0.9991679,0.00005689519,0.00005450361,0.0003749787,0.0002184188,0.0001273037],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"observational","study_design_gemma":"observational","study_design_scores_codex":[0.04785403,0.001376897,0.9355731,0.0002618587,0.0001787345,0.001921537,0.0001267597,0.00005736548,0.003490242,0.00003358572,0.0004839017,0.008641974],"study_design_scores_gemma":[0.008046249,0.0125202,0.9653639,0.00004083872,0.00007507487,0.000097574,0.000008095155,0.00005616174,0.0003602017,0.000006047992,0.01332141,0.0001042388],"study_design_candidate":"observational","study_design_consensus":"observational","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9980783,0.0003816835,0.00001313666,0.0004793734,0.0001739209,0.0004602993,0.000005027247,0.00001080024,0.0003973979],"genre_scores_gemma":[0.9983907,0.0005397808,0.0001456523,0.0006841238,0.00004323202,0.000006307054,0.00004186055,0.00002987436,0.0001184683],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.03980778,"threshold_uncertainty_score":0.4569838,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.01418266176272482,"score_gpt":0.2698115353049822,"score_spread":0.2556288735422574,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}