{"id":"W3203864936","doi":"10.1212/wnl.96.15_supplement.2240","title":"SUNFISH Part 2: 24-month Efficacy and Safety of Risdiplam in Patients with Type 2 or Non-ambulant Type 3 Spinal Muscular Atrophy (SMA) (2240)","year":2021,"lang":"en","type":"article","venue":"Neurology","topic":"Neurogenetic and Muscular Disorders Research","field":"Medicine","cited_by":2,"is_retracted":false,"has_abstract":true,"ca_institutions":"McGill University","funders":"","keywords":"SMA*; Spinal muscular atrophy; Medicine; Physical medicine and rehabilitation; Atrophy; Physical therapy; Pediatrics; Internal medicine; Disease","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0005652859,0.000566231,0.001265398,0.0003259065,0.0002800446,0.0002592818,0.0003751148,0.0007746358,0.003633077],"category_scores_gemma":[0.0004133206,0.0001715601,0.001027457,0.0002273696,0.0002638856,0.000283615,0.0001361255,0.0008192527,0.0006905668],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0005370644,"about_ca_system_score_gemma":0.0005423119,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.0009247375,"about_ca_topic_score_gemma":0.001830863,"domain_scores_codex":[0.9998585,0.00005087677,0.00001544865,0.00002246854,0.0000202036,0.00003242216],"domain_scores_gemma":[0.9996254,0.00004763951,0.0000920264,0.00003832538,0.00004557123,0.0001510724],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"randomized_trial","study_design_gemma":"observational","study_design_scores_codex":[0.6363004,0.02985601,0.04272718,0.001532393,0.002782445,0.001108155,0.0002440906,0.001255574,0.09044082,0.000123279,0.004738451,0.1888912],"study_design_scores_gemma":[0.1866015,0.5751832,0.2157257,0.0001201745,0.001433247,0.001132643,0.0001036346,0.0008482712,0.01438164,0.00009515561,0.004303426,0.00007146291],"study_design_candidate":"observational","study_design_consensus":null,"genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9948305,0.002292127,0.0001521109,0.0001156534,0.00003713568,0.0005345639,0.0008873513,0.0000382717,0.001112285],"genre_scores_gemma":[0.9932139,0.001121854,0.0005213685,0.0004168944,0.00005597814,0.0006191593,0.001705239,0.00001036817,0.002335208],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.003633077,"threshold_uncertainty_score":0.01215386,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.01418266176272482,"score_gpt":0.2698115353049822,"score_spread":0.2556288735422574,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}