{"id":"W3204294498","doi":"10.51731/cjht.2021.167","title":"Onasemnogene Abeparvovec (Zolgensma)","year":2021,"lang":"en","type":"article","venue":"Canadian Journal of Health Technologies","topic":"Neurogenetic and Muscular Disorders Research","field":"Medicine","cited_by":3,"is_retracted":false,"has_abstract":true,"ca_institutions":"","funders":"","keywords":"SMN1; SMA*; Spinal muscular atrophy; Medicine; Family medicine; Food and drug administration; Expert opinion; Intensive care medicine; Medical emergency","routes":{"ca_aff":false,"ca_fund":false,"ca_venue":false,"about_ca":true,"invisible_to_affiliation_only":true},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.001593361,0.0002833293,0.0004476387,0.0007156293,0.0009902861,0.001601195,0.0007283037,0.002926505,0.03239877],"category_scores_gemma":[0.003202738,0.0001981351,0.0005961606,0.0004803096,0.0005433389,0.0005426976,0.0006806614,0.003345733,0.006486478],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.005199029,"about_ca_system_score_gemma":0.01012422,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.09102369,"about_ca_topic_score_gemma":0.2834693,"domain_scores_codex":[0.9990351,0.0001338583,0.00004267295,0.00008972747,0.0005147328,0.0001839403],"domain_scores_gemma":[0.9982662,0.0002732353,0.0001150161,0.000048137,0.0007952804,0.0005021797],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"not_applicable","study_design_gemma":"not_applicable","study_design_scores_codex":[0.001899799,0.0001748156,0.001407511,0.000540154,0.00004762142,0.0006155685,0.00009307118,0.0001655639,0.004181878,0.007219152,0.7220244,0.2616304],"study_design_scores_gemma":[0.0004132113,0.0001848862,0.001790211,0.0002362141,0.00003449493,0.0002603584,0.00002916233,0.000109322,0.0009816434,0.0003647495,0.9955848,0.00001096164],"study_design_candidate":"not_applicable","study_design_consensus":"not_applicable","genre_codex":"other","genre_gemma":"other","genre_scores_codex":[0.0303019,0.1351331,0.004560938,0.24843,0.01911638,0.001939717,0.02167903,0.002582459,0.5362564],"genre_scores_gemma":[0.163906,0.0658904,0.01203394,0.1732649,0.003562416,0.0007056636,0.01754524,0.000508725,0.5625827],"genre_candidate":"other","genre_consensus":"other","teacher_disagreement_score":0.09102369,"threshold_uncertainty_score":0.1809877,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.03993663346816206,"score_gpt":0.3234640521587164,"score_spread":0.2835274186905544,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}