{"id":"W3211760408","doi":"10.1182/blood-2021-150541","title":"Follow-up of More Than 5 Years in a Cohort of Patients with Hemophilia B Treated with Fidanacogene Elaparvovec Adeno-Associated Virus Gene Therapy","year":2021,"lang":"en","type":"article","venue":"Blood","topic":"Hemophilia Treatment and Research","field":"Medicine","cited_by":27,"is_retracted":false,"has_abstract":true,"ca_institutions":"University of Toronto; St. Michael's Hospital","funders":"","keywords":"Medicine; Adverse effect; Internal medicine; Cohort; Pediatrics; Surgery","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0005976663,0.0002917881,0.0005737079,0.0008461359,0.001249598,0.0009703176,0.0002986165,0.0007398863,0.001216478],"category_scores_gemma":[0.001410418,0.0002755136,0.0006912558,0.0009635965,0.0003079015,0.0008834868,0.0005242657,0.001000024,0.0002736027],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0003839918,"about_ca_system_score_gemma":0.0003166946,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.003735503,"about_ca_topic_score_gemma":0.002574528,"domain_scores_codex":[0.9995993,0.00008246869,0.00004283425,0.0001056683,0.00006231859,0.0001074508],"domain_scores_gemma":[0.9988833,0.0001537626,0.0004704494,0.00007344148,0.0001031952,0.0003157409],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"observational","study_design_gemma":"observational","study_design_scores_codex":[0.0004827314,0.0001399161,0.996128,0.000006372758,0.00006542948,0.0007710072,0.0001354305,0.00004976544,0.0003802803,0.00002016288,0.0001145924,0.001706299],"study_design_scores_gemma":[0.00005776262,0.0008377669,0.9956949,0.00001226948,0.0001100894,0.001808629,0.0003075365,0.0002562313,0.00009966655,0.0000380157,0.0007642349,0.00001280371],"study_design_candidate":"observational","study_design_consensus":"observational","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9987926,0.0003686282,0.00006153634,0.00006505033,0.00001094895,0.00001397964,0.0002022895,0.000002567552,0.0004823136],"genre_scores_gemma":[0.9990575,0.0001391991,0.00004438514,0.00007696394,0.00002115871,0.00001365861,0.0003971126,0.000001699672,0.0002483266],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.003735503,"threshold_uncertainty_score":0.007427514,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.01297443137248601,"score_gpt":0.250546902525979,"score_spread":0.237572471153493,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}