{"id":"W4206712987","doi":"10.1017/cjn.2021.407","title":"P.131 Outcomes of Nusinersen in adult and pediatric cohorts of spinal muscular amyotrophy after two years of usage at the CHU de Québec-Université Laval","year":2021,"lang":"en","type":"article","venue":"Canadian Journal of Neurological Sciences / Journal Canadien des Sciences Neurologiques","topic":"Neurogenetic and Muscular Disorders Research","field":"Medicine","cited_by":0,"is_retracted":false,"has_abstract":true,"ca_institutions":"Héma-Québec","funders":"","keywords":"Medicine; Spinal muscular atrophy; Pediatrics; Tolerability; Physical therapy; Disease; Adverse effect; Internal medicine","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":true,"about_ca":true,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0007020259,0.000196748,0.0004054406,0.0003737926,0.0005881747,0.0005190614,0.0002443178,0.0002932392,0.002246473],"category_scores_gemma":[0.001597721,0.00006350868,0.0005003692,0.0006282859,0.0002783251,0.0003507689,0.0003097172,0.00050933,0.0003609945],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.001409582,"about_ca_system_score_gemma":0.001230649,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.05440615,"about_ca_topic_score_gemma":0.05369736,"domain_scores_codex":[0.9996163,0.00005179026,0.00002173648,0.00005311316,0.0001100698,0.0001470347],"domain_scores_gemma":[0.998212,0.0002118445,0.0006594242,0.00006095694,0.0004067652,0.0004489916],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"observational","study_design_gemma":"observational","study_design_scores_codex":[0.002303605,0.0002253067,0.9847974,0.00005391701,0.0001163431,0.0007308198,0.0002801157,0.00009399582,0.0003308663,0.00004542009,0.0007810588,0.01024106],"study_design_scores_gemma":[0.00003841436,0.001657935,0.9966354,0.00002607083,0.0000354861,0.0005062079,0.0002803804,0.00006747913,0.0000696798,0.00001731473,0.000658425,0.000007150067],"study_design_candidate":"observational","study_design_consensus":"observational","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9968588,0.001000586,0.00003112603,0.0000672017,0.000009431242,0.00003219712,0.0009718427,0.000002840086,0.00102607],"genre_scores_gemma":[0.9976602,0.0002976398,0.00003448554,0.0000483927,0.00001120371,0.00001972608,0.001328776,0.000002121706,0.0005975648],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.05440615,"threshold_uncertainty_score":0.1081789,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.01507547309663301,"score_gpt":0.2645623819982644,"score_spread":0.2494869089016314,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}