{"id":"W4214598407","doi":"10.1016/j.nmd.2022.02.012","title":"Functional outcome measures in young, steroid-naïve boys with Duchenne muscular dystrophy","year":2022,"lang":"en","type":"article","venue":"Neuromuscular Disorders","topic":"Muscle Physiology and Disorders","field":"Biochemistry, Genetics and Molecular Biology","cited_by":9,"is_retracted":false,"has_abstract":true,"ca_institutions":"Children's Hospital of Eastern Ontario; University of Ottawa; London Health Sciences Centre; Alberta Children's Hospital","funders":"National Institutes of Health; Italfarmaco; Voyager Therapeutics; Amicus Therapeutics; PTC Therapeutics; Muscular Dystrophy Canada; National Institute of Neurological Disorders and Stroke; Charcot-Marie-Tooth Association; FSH Society; Cure SMA; Muscular Dystrophy Association; Neurocrine Biosciences; FibroGen; Fondazione Telethon; Action Duchenne; AstraZeneca; Parent Project Muscular Dystrophy; AveXis; Pfizer; Biogen; Acceleron; American Brain Foundation; Eli Lilly and Company; Sarepta Therapeutics; Jain Foundation; Foundation for the National Institutes of Health","keywords":"Duchenne muscular dystrophy; Ambulatory; Medicine; Physical therapy; Population; Physical medicine and rehabilitation; Internal medicine","routes":{"ca_aff":true,"ca_fund":true,"ca_venue":false,"about_ca":true,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0006037758,0.0003426425,0.0005089384,0.0007718951,0.0003030693,0.0003248069,0.0002606552,0.0003627192,0.0007444978],"category_scores_gemma":[0.002735965,0.0001232477,0.0002369633,0.0003199061,0.00038214,0.0003456316,0.0003138848,0.000345541,0.0002645663],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0002832683,"about_ca_system_score_gemma":0.0001866658,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.003539929,"about_ca_topic_score_gemma":0.004453351,"domain_scores_codex":[0.9995031,0.0001514444,0.00005142852,0.00007617318,0.0001401869,0.00007755149],"domain_scores_gemma":[0.9983757,0.0004316585,0.0005986575,0.00005364671,0.0002175152,0.0003227692],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"observational","study_design_gemma":"observational","study_design_scores_codex":[0.0001497137,0.00008800634,0.9953566,0.00001893545,0.00001692728,0.0003733765,0.0002924006,0.00006757887,0.0005790414,0.000006831599,0.00005251291,0.002998077],"study_design_scores_gemma":[0.000005611943,0.0004942979,0.9987219,0.000003431592,0.000007149351,0.0004168758,0.0001467763,0.00003086663,0.0001102261,0.0000043107,0.00005645211,0.000002065346],"study_design_candidate":"observational","study_design_consensus":"observational","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9995097,0.0001984173,0.00003103052,0.000007066212,0.0000019359,0.000005244612,0.00008815242,0.000002485845,0.0001560922],"genre_scores_gemma":[0.9994412,0.00008078328,0.00007742439,0.0000134202,0.000005122388,0.000008902901,0.0002073607,0.000001474805,0.0001643549],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.003539929,"threshold_uncertainty_score":0.007038653,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.01056610987404101,"score_gpt":0.2134090327334458,"score_spread":0.2028429228594048,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}