{"id":"W4220848736","doi":"10.1007/s43441-022-00389-x","title":"Unmet Therapeutic Needs of Non-Ambulatory Patients with Duchenne Muscular Dystrophy: A Mixed-Method Analysis","year":2022,"lang":"en","type":"article","venue":"Therapeutic Innovation & Regulatory Science","topic":"Muscle Physiology and Disorders","field":"Biochemistry, Genetics and Molecular Biology","cited_by":7,"is_retracted":false,"has_abstract":false,"ca_institutions":"","funders":"Duchenne Research Fund; Muscular Dystrophy Canada; Parent Project Muscular Dystrophy; Pfizer","keywords":"Medicine; Ambulatory; Duchenne muscular dystrophy; Prom; Quality of life (healthcare); Context (archaeology); Population; Physical therapy; Muscular dystrophy; Internal medicine; Nursing","routes":{"ca_aff":false,"ca_fund":true,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":true},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.004425881,0.0004520359,0.0009412984,0.001588755,0.0007509653,0.001520995,0.001026992,0.0007319758,0.004507267],"category_scores_gemma":[0.01596996,0.0002825594,0.0021166,0.001574055,0.0004191642,0.0008445667,0.00230001,0.0007818603,0.000458437],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.001004546,"about_ca_system_score_gemma":0.001037455,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.003759969,"about_ca_topic_score_gemma":0.006027955,"domain_scores_codex":[0.9945028,0.003471202,0.0005071153,0.0004718936,0.0005086454,0.0005383983],"domain_scores_gemma":[0.989869,0.006529229,0.001769417,0.0005365069,0.0007554805,0.0005404217],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"observational","study_design_gemma":"qualitative","study_design_scores_codex":[0.003178931,0.000377267,0.9788382,0.0001801207,0.001110117,0.0001685246,0.001651558,0.0003146488,0.0003453698,0.0003702045,0.0004375777,0.0130274],"study_design_scores_gemma":[0.0001516758,0.001048625,0.9842085,0.00008944268,0.0005279472,0.0007607045,0.006627972,0.004441136,0.0002449992,0.0007189393,0.001135015,0.00004496127],"study_design_candidate":"qualitative","study_design_consensus":null,"genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.99755,0.0002390694,0.0006443141,0.0000785704,0.000008012644,0.00005371543,0.0008154633,0.000006050569,0.0006048616],"genre_scores_gemma":[0.9982988,0.00005581739,0.0005635452,0.00003458421,0.000007386572,0.0001207736,0.0005681688,0.000008429939,0.0003424418],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.004507267,"threshold_uncertainty_score":0.02340657,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.006282202508077043,"score_gpt":0.2479442496999644,"score_spread":0.2416620471918874,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}