{"id":"W4231586227","doi":"10.1016/j.nmd.2020.08.284","title":"DMD – THERAPY","year":2020,"lang":"en","type":"article","venue":"Neuromuscular Disorders","topic":"CRISPR and Genetic Engineering","field":"Biochemistry, Genetics and Molecular Biology","cited_by":0,"is_retracted":false,"has_abstract":false,"ca_institutions":"Hospital for Sick Children","funders":"","keywords":"Dystrophin; Myogenesis; Duchenne muscular dystrophy; CRISPR; Biology; HEK 293 cells; Utrophin; Reprogramming; Cell biology; Muscular dystrophy; mdx mouse; Genome editing; Bioinformatics; Computational biology; Genetics; Gene; Myocyte","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"codex-gemma-dda1882f352a","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.00002611358,0.0001153519,0.00007561847,0.00001204906,0.0000344916,0.00001346282,0.0001470281,0.00005368544,0.00003786429],"category_scores_gemma":[0.00003540818,0.0001149082,0.0001062587,0.00007791786,0.00002371469,0.000001355754,0.00004579388,0.00006315143,0.00002343568],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.000001102968,"about_ca_system_score_gemma":0.00001281068,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.000003418965,"about_ca_topic_score_gemma":0.000004144837,"domain_scores_codex":[0.9993747,0.00002064667,0.00008513488,0.0002679365,0.00009045179,0.0001611092],"domain_scores_gemma":[0.9996775,0.000002725235,0.00001482913,0.0001999915,0.00001216389,0.00009277662],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"bench_or_experimental","study_design_gemma":"not_applicable","study_design_scores_codex":[0.00004423604,0.00003685124,0.002459557,0.00001509084,0.00004562431,0.000002770002,0.0001119663,0.002150526,0.9584092,0.00003298179,0.003424417,0.03326672],"study_design_scores_gemma":[0.0009778563,0.0005320791,0.009617029,0.000002041138,0.000009028502,0.000003212981,0.00005641233,0.0004851844,0.1481196,0.00003491696,0.8398582,0.0003043971],"study_design_candidate":"bench_or_experimental","study_design_consensus":null,"genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9731484,0.002831424,0.01931897,0.002037144,0.0001603779,0.0001994658,0.00000406305,0.00005443588,0.002245742],"genre_scores_gemma":[0.996209,0.001331307,0.0002143024,0.00197176,0.0001535403,0.00001056279,0.00002548347,0.00003103717,0.00005306488],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.8364338,"threshold_uncertainty_score":0.4685819,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.008884208831898223,"score_gpt":0.2628504436723857,"score_spread":0.2539662348404875,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}