{"id":"W4242565444","doi":"10.1016/j.nmd.2020.08.174","title":"SMA: REGISTRIES, BIOMARKERS &amp; OUTCOME MEASURES","year":2020,"lang":"en","type":"article","venue":"Neuromuscular Disorders","topic":"Neurogenetic and Muscular Disorders Research","field":"Medicine","cited_by":1,"is_retracted":false,"has_abstract":false,"ca_institutions":"University of Ottawa","funders":"","keywords":"SMA*; Medicine; Clinical trial; Spinal muscular atrophy; Disease; Family medicine; Internal medicine","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"codex-gemma-dda1882f352a","candidate_categories":["metaepi_narrow"],"consensus_categories":[],"category_scores_codex":[0.0002107389,0.0003655968,0.0005059271,0.0001467363,0.000172623,0.00005738585,0.000347618,0.0001464554,0.0003559134],"category_scores_gemma":[0.001060523,0.0003372405,0.0005344998,0.0007931493,0.0002989675,0.00007629958,0.0001560226,0.0004925315,0.0003856524],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0000295633,"about_ca_system_score_gemma":0.0001843576,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.00008818496,"about_ca_topic_score_gemma":0.0000668492,"domain_scores_codex":[0.9968508,0.0001844683,0.0004594317,0.000821344,0.001038984,0.0006450071],"domain_scores_gemma":[0.9982787,0.00005590325,0.00008578076,0.0007818001,0.0001138423,0.0006840184],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"observational","study_design_gemma":"not_applicable","study_design_scores_codex":[0.002332724,0.001461536,0.6400589,0.001778065,0.002404218,0.0006677946,0.00138746,0.0001946737,0.07692531,0.0007815569,0.09397759,0.1780301],"study_design_scores_gemma":[0.003588977,0.0004735249,0.05690409,0.0000220689,0.0002954257,0.00005165737,0.0001817831,0.000167533,0.0006290641,0.0001029052,0.9371392,0.0004438156],"study_design_candidate":"not_applicable","study_design_consensus":null,"genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.850762,0.00868176,0.01094584,0.09837522,0.0005198299,0.003341741,0.00003841536,0.0009223184,0.02641294],"genre_scores_gemma":[0.9897624,0.001386577,0.0007297274,0.007053646,0.0001216826,0.00006446017,0.00008771179,0.0001367775,0.0006570102],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.8431616,"threshold_uncertainty_score":0.999908,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.08605660657254435,"score_gpt":0.3202702478818111,"score_spread":0.2342136413092667,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}