{"id":"W4290830384","doi":"10.1136/jnnp-2022-abn2.232","title":"188 SUNFISH 3-year efficacy and safety of risdiplam in types 2 and 3 SMA","year":2022,"lang":"en","type":"article","venue":"Journal of Neurology Neurosurgery & Psychiatry","topic":"Neurogenetic and Muscular Disorders Research","field":"Medicine","cited_by":1,"is_retracted":false,"has_abstract":true,"ca_institutions":"McGill University","funders":"","keywords":"SMA*; Medicine; Placebo; Spinal muscular atrophy; Population; Clinical trial; Motor function; Physical therapy; Internal medicine; Pediatrics; Physical medicine and rehabilitation","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"codex-gemma-dda1882f352a","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0005914312,0.0001353684,0.0005076354,0.0004821434,0.00008423613,0.000007476822,0.0001163342,0.00006578292,0.00009676178],"category_scores_gemma":[0.0001917974,0.0001260861,0.0001224814,0.0003229256,0.0001888717,0.00004173698,0.0001460422,0.0009511348,6.914802e-7],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.000006147216,"about_ca_system_score_gemma":0.0002248082,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.000005768416,"about_ca_topic_score_gemma":0.00000523024,"domain_scores_codex":[0.9980888,0.0004066975,0.0006326379,0.0002484442,0.000365533,0.0002579309],"domain_scores_gemma":[0.9989976,0.0002976379,0.0002858814,0.0002008682,0.00006375233,0.0001542859],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"observational","study_design_gemma":"observational","study_design_scores_codex":[0.005091775,0.0005886761,0.9843013,0.00008635342,0.00005890926,0.0005076341,0.00007423946,0.00007181968,0.004379658,0.00009367736,0.002585374,0.002160531],"study_design_scores_gemma":[0.003820328,0.002724637,0.976095,0.00002041933,0.00006979713,0.004432046,0.00005899885,0.00002973615,0.0000646339,0.0001853652,0.01241494,0.00008415674],"study_design_candidate":"observational","study_design_consensus":"observational","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9863555,0.002458819,0.000002700742,0.009863888,0.0008648589,0.000200415,0.000006355261,0.000006045125,0.0002414449],"genre_scores_gemma":[0.9954739,0.001864418,0.00006778683,0.002421716,0.000096271,0.000003104236,0.000001243432,0.00002780497,0.0000438003],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.009829569,"threshold_uncertainty_score":0.5141644,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.01071879857524039,"score_gpt":0.2666357938498909,"score_spread":0.2559169952746505,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}