{"id":"W4290830471","doi":"10.1136/jnnp-2022-abn2.231","title":"187 SUNFISH Part 2: 24-month efficacy of risdiplam compared with external control comparators","year":2022,"lang":"en","type":"article","venue":"Journal of Neurology Neurosurgery & Psychiatry","topic":"Neurogenetic and Muscular Disorders Research","field":"Medicine","cited_by":1,"is_retracted":false,"has_abstract":true,"ca_institutions":"McGill University","funders":"","keywords":"SMA*; Placebo; Medicine; Spinal muscular atrophy; Population; Motor function; Internal medicine; Physical therapy; Physical medicine and rehabilitation; Pathology; Disease","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.003259001,0.002138779,0.004637605,0.0008059154,0.0003445857,0.001208868,0.001016535,0.001646758,0.01452139],"category_scores_gemma":[0.004315307,0.0005871626,0.00602319,0.0005879118,0.0006432848,0.001266909,0.0006842343,0.0030785,0.001981594],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.000631581,"about_ca_system_score_gemma":0.0006519479,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.0004315603,"about_ca_topic_score_gemma":0.000884702,"domain_scores_codex":[0.9975086,0.001394208,0.0002004607,0.0003954911,0.0002701641,0.0002309561],"domain_scores_gemma":[0.9969696,0.00110175,0.001051881,0.0003000993,0.0002767535,0.0002997961],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"randomized_trial","study_design_gemma":"observational","study_design_scores_codex":[0.9777083,0.002955362,0.001359427,0.0008734694,0.004091667,0.00002490642,0.00003445186,0.0004712072,0.001854858,0.00006435031,0.000956035,0.009606055],"study_design_scores_gemma":[0.5428756,0.3983099,0.03694027,0.0002160292,0.009636111,0.0001426812,0.00009609221,0.001919278,0.003825977,0.0005580392,0.005391411,0.0000885949],"study_design_candidate":"observational","study_design_consensus":null,"genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9676459,0.008067427,0.001238923,0.0003774764,0.0005426327,0.005226398,0.01211022,0.0002857619,0.004505207],"genre_scores_gemma":[0.9746431,0.001837042,0.001805385,0.0005258494,0.0004196541,0.007420539,0.008817304,0.00007186758,0.004459197],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.01452139,"threshold_uncertainty_score":0.04857892,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.01715619347231028,"score_gpt":0.2714304271336868,"score_spread":0.2542742336613765,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}